Automated design of hammerhead ribozymes and validation by targeting the PABPN1 gene transcript

por Kharma, Nawwaf, Varin, Luc, Abu-Baker, Aida, Ouellet, Jonathan, Najeh, Sabrine, Ehdaeivand, Mohammad-Reza, Belmonte, Gabriel, Ambri, Anas, Rouleau, Guy, Perreault, Jonathan
Publicado 2016

RNA-Based Therapy Utilizing Oculopharyngeal Muscular Dystrophy Transcript Knockdown and Replacement

por Abu-Baker, Aida, Kharma, Nawwaf, Perreault, Jonathan, Grant, Alanna, Shekarabi, Masoud, Maios, Claudia, Dona, Michele, Neri, Christian, Dion, Patrick A., Parker, Alex, Varin, Luc, Rouleau, Guy A.
Publicado 2019