Corrigendum: Targeted Gene Delivery: Where to Land

por Pavani, Giulia, Amendola, Mario
Publicado 2021

Targeted Gene Delivery: Where to Land

por Pavani, Giulia, Amendola, Mario
Publicado 2021

Disorder and Public Concern Around Globalization

por Amendola, Mario, Gaffard, Jean-Luc
Publicado 2019

CRISPRthripsis: The Risk of CRISPR/Cas9-induced Chromothripsis in Gene Therapy

por Amendola, Mario, Brusson, Mégane, Miccio, Annarita
Publicado 2022

Easy quantitative assessment of genome editing by sequence trace decomposition

por Brinkman, Eva K., Chen, Tao, Amendola, Mario, van Steensel, Bas
Publicado 2014

GATA Factor-Mediated Gene Regulation in Human Erythropoiesis

por Romano, Oriana, Petiti, Luca, Felix, Tristan, Meneghini, Vasco, Portafax, Michel, Antoniani, Chiara, Amendola, Mario, Bicciato, Silvio, Peano, Clelia, Miccio, Annarita
Publicado 2020

Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins

por Pavani, Giulia, Laurent, Marine, Fabiano, Anna, Cantelli, Erika, Sakkal, Aboud, Corre, Guillaume, Lenting, Peter J., Concordet, Jean-Paul, Toueille, Magali, Miccio, Annarita, Amendola, Mario
Publicado 2020

Author Correction: Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins

por Pavani, Giulia, Laurent, Marine, Fabiano, Anna, Cantelli, Erika, Sakkal, Aboud, Corre, Guillaume, Lenting, Peter J., Concordet, Jean-Paul, Toueille, Magali, Miccio, Annarita, Amendola, Mario
Publicado 2020

The Cohesin Release Factor WAPL Restricts Chromatin Loop Extension

por Haarhuis, Judith H.I., van der Weide, Robin H., Blomen, Vincent A., Yáñez-Cuna, J. Omar, Amendola, Mario, van Ruiten, Marjon S., Krijger, Peter H.L., Teunissen, Hans, Medema, René H., van Steensel, Bas, Brummelkamp, Thijn R., de Wit, Elzo, Rowland, Benjamin D.
Publicado 2017

Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype

por Weber, Leslie, Frati, Giacomo, Felix, Tristan, Hardouin, Giulia, Casini, Antonio, Wollenschlaeger, Clara, Meneghini, Vasco, Masson, Cecile, De Cian, Anne, Chalumeau, Anne, Mavilio, Fulvio, Amendola, Mario, Andre-Schmutz, Isabelle, Cereseto, Anna, El Nemer, Wassim, Concordet, Jean-Paul, Giovannangeli, Carine, Cavazzana, Marina, Miccio, Annarita
Publicado 2020

Base-editing-mediated dissection of a γ-globin cis-regulatory element for the therapeutic reactivation of fetal hemoglobin expression

por Antoniou, Panagiotis, Hardouin, Giulia, Martinucci, Pierre, Frati, Giacomo, Felix, Tristan, Chalumeau, Anne, Fontana, Letizia, Martin, Jeanne, Masson, Cecile, Brusson, Megane, Maule, Giulia, Rosello, Marion, Giovannangeli, Carine, Abramowski, Vincent, de Villartay, Jean-Pierre, Concordet, Jean-Paul, Del Bene, Filippo, El Nemer, Wassim, Amendola, Mario, Cavazzana, Marina, Cereseto, Anna, Romano, Oriana, Miccio, Annarita
Publicado 2022