Spinal Muscular Atrophy Treatment in Patients Identified by Newborn Screening—A Systematic Review

por Aragon-Gawinska, Karolina, Mouraux, Charlotte, Dangouloff, Tamara, Servais, Laurent
Publicado 2023

Response of plasma microRNAs to nusinersen treatment in patients with SMA

por Zaharieva, Irina T., Scoto, Mariacristina, Aragon‐Gawinska, Karolina, Ridout, Deborah, Doreste, Bruno, Servais, Laurent, Muntoni, Francesco, Zhou, Haiyan
Publicado 2022

Long-term nusinersen treatment across a wide spectrum of spinal muscular atrophy severity: a real-world experience

por Łusakowska, Anna, Wójcik, Adrianna, Frączek, Anna, Aragon-Gawińska, Karolina, Potulska-Chromik, Anna, Baranowski, Paweł, Nowak, Ryszard, Rosiak, Grzegorz, Milczarek, Krzysztof, Konecki, Dariusz, Gierlak-Wójcicka, Zuzanna, Burlewicz, Małgorzata, Kostera-Pruszczyk, Anna
Publicado 2023