Biology of adeno-associated viral vectors in the central nervous system

por Murlidharan, Giridhar, Samulski, Richard J., Asokan, Aravind
Publicado 2014

Intra- and Inter-Subunit Disulfide Bond Formation Is Nonessential in Adeno-Associated Viral Capsids

por Pulicherla, Nagesh, Kota, Pradeep, Dokholyan, Nikolay V., Asokan, Aravind
Publicado 2012

Physical positioning markedly enhances brain transduction after intrathecal AAV9 infusion

por Castle, Michael J., Cheng, Yuhsiang, Asokan, Aravind, Tuszynski, Mark H.
Publicado 2018

Interplay between Furin and Sialoglycans in Modulating Adeno-Associated Viral Cell Entry

por Smith, Timothy J., Fusco, Robert M., Elmore, Zachary C., Asokan, Aravind
Publicado 2023

Bocavirus Episome in Infected Human Tissue Contains Non-Identical Termini

por Kapoor, Amit, Hornig, Mady, Asokan, Aravind, Williams, Brent, Henriquez, Jose A., Lipkin, W. Ian
Publicado 2011

Rescuing AAV gene transfer from neutralizing antibodies with an IgG-degrading enzyme

por Elmore, Zachary C., Oh, Daniel K., Simon, Katherine E., Fanous, Marco M., Asokan, Aravind
Publicado 2020

Preclinical toxicity evaluation of AAV for pain: evidence from human AAV studies and from the pharmacology of analgesic drugs

por Pleticha, Josef, Heilmann, Lukas F, Evans, Christopher H, Asokan, Aravind, Samulski, Richard Jude, Beutler, Andreas S
Publicado 2014

Epigenetic Silencing of Recombinant Adeno-associated Virus Genomes by NP220 and the HUSH Complex

por Das, Anshuman, Vijayan, Madhuvanthi, Walton, Eric M., Stafford, V. Grace, Fiflis, David N., Asokan, Aravind
Publicado 2022

Controlling mRNA stability and translation with the CRISPR endoribonuclease Csy4

por Borchardt, Erin K., Vandoros, Leonidas A., Huang, Michael, Lackey, Patrick E., Marzluff, William F., Asokan, Aravind
Publicado 2015

CNS-restricted Transduction and CRISPR/Cas9-mediated Gene Deletion with an Engineered AAV Vector

por Murlidharan, Giridhar, Sakamoto, Kensuke, Rao, Lavanya, Corriher, Travis, Wang, Dan, Gao, Guangping, Sullivan, Patrick, Asokan, Aravind
Publicado 2016

Tissue-Dependent Expression and Translation of Circular RNAs with Recombinant AAV Vectors In Vivo

por Meganck, Rita M., Borchardt, Erin K., Castellanos Rivera, Ruth M., Scalabrino, Miranda L., Wilusz, Jeremy E., Marzluff, William F., Asokan, Aravind
Publicado 2018

In Vivo Gene Editing of Muscle Stem Cells with Adeno-Associated Viral Vectors in a Mouse Model of Duchenne Muscular Dystrophy

por Kwon, Jennifer B., Ettyreddy, Adarsh R., Vankara, Ashish, Bohning, Joel D., Devlin, Garth, Hauschka, Stephen D., Asokan, Aravind, Gersbach, Charles A.
Publicado 2020

Receptor Switching in Newly Evolved Adeno-associated Viruses

por Havlik, L. Patrick, Das, Anshuman, Mietzsch, Mario, Oh, Daniel K., Ark, Jonathan, McKenna, Robert, Agbandje-McKenna, Mavis, Asokan, Aravind
Publicado 2021

The membrane associated accessory protein is an adeno-associated viral egress factor

por Elmore, Zachary C., Patrick Havlik, L., Oh, Daniel K., Anderson, Leif, Daaboul, George, Devlin, Garth W., Vincent, Heather A., Asokan, Aravind
Publicado 2021

AAV Gene Therapy for MPS1-associated Corneal Blindness

por Vance, Melisa, Llanga, Telmo, Bennett, Will, Woodard, Kenton, Murlidharan, Giridhar, Chungfat, Neil, Asokan, Aravind, Gilger, Brian, Kurtzberg, Joanne, Samulski, R. Jude, Hirsch, Matthew L.
Publicado 2016

Gene Therapy: Will the Promise of Optimizing Lung Allografts Become Reality?

por Gao, Qimeng, DeLaura, Isabel F., Anwar, Imran J., Kesseli, Samuel J., Kahan, Riley, Abraham, Nader, Asokan, Aravind, Barbas, Andrew S., Hartwig, Matthew G.
Publicado 2022

AAV Gene Augmentation of Truncated Complement Factor H Differentially Rescues Ocular Complement Dysregulation in a Mouse Model

por Grigsby, Daniel, Klingeborn, Mikael, Kelly, Una, Chew, Lindsey A., Asokan, Aravind, Devlin, Garth, Smith, Sharon, Keyes, Lisa, Timmers, Adrian, Scaria, Abraham, Bowes Rickman, Catherine
Publicado 2023

An siRNA Screen Identifies the U2 snRNP Spliceosome as a Host Restriction Factor for Recombinant Adeno-associated Viruses

por Schreiber, Claire A., Sakuma, Toshie, Izumiya, Yoshihiro, Holditch, Sara J., Hickey, Raymond D., Bressin, Robert K., Basu, Upamanyu, Koide, Kazunori, Asokan, Aravind, Ikeda, Yasuhiro
Publicado 2015

Inducing circular RNA formation using the CRISPR endoribonuclease Csy4

por Borchardt, Erin K., Meganck, Rita M., Vincent, Heather A., Ball, Christopher B., Ramos, Silvia B.V., Moorman, Nathaniel J., Marzluff, William F., Asokan, Aravind
Publicado 2017

The Golgi Calcium ATPase Pump Plays an Essential Role in Adeno-associated Virus Trafficking and Transduction

por Madigan, Victoria J., Berry, Garrett E., Tyson, Tyne O., Nardone-White, Dasean, Ark, Jonathan, Elmore, Zachary C., Murlidharan, Giridhar, Vincent, Heather A., Asokan, Aravind
Publicado 2020