High value of (64)Cu as a tool to evaluate the restoration of physiological copper excretion after gene therapy in Wilson’s disease

por Murillo, Oihana, Collantes, Maria, Gazquez, Cristina, Moreno, Daniel, Hernandez-Alcoceba, Ruben, Barberia, Miren, Ecay, Margarita, Tamarit, Blanche, Douar, Anne, Ferrer, Veronica, Combal, Jean Philippe, Peñuelas, Ivan, Bénichou, Bernard, Gonzalez-Aseguinolaza, Gloria
Publicado 2022

CRISPR/Cas9-mediated glycolate oxidase disruption is an efficacious and safe treatment for primary hyperoxaluria type I

por Zabaleta, Nerea, Barberia, Miren, Martin-Higueras, Cristina, Zapata-Linares, Natalia, Betancor, Isabel, Rodriguez, Saray, Martinez-Turrillas, Rebeca, Torella, Laura, Vales, Africa, Olagüe, Cristina, Vilas-Zornoza, Amaia, Castro-Labrador, Laura, Lara-Astiaso, David, Prosper, Felipe, Salido, Eduardo, Gonzalez-Aseguinolaza, Gloria, Rodriguez-Madoz, Juan R.
Publicado 2018