Stem cells set their sights on retinitis pigmentosa

por Bennicelli, Jeannette L, Bennett, Jean
Publicado 2013

Antisense Oligonucleotide (AON)-based Therapy for Leber Congenital Amaurosis Caused by a Frequent Mutation in CEP290

por Collin, Rob WJ, den Hollander, Anneke I, van der Velde-Visser, Saskia D, Bennicelli, Jeannette, Bennett, Jean, Cremers, Frans PM
Publicado 2012

An Autogenously Regulated Expression System for Gene Therapeutic Ocular Applications

por Sochor, Matthew A., Vasireddy, Vidyullatha, Drivas, Theodore G., Wojno, Adam, Doung, Thu, Shpylchak, Ivan, Bennicelli, Jeannette, Chung, Daniel, Bennett, Jean, Lewis, Mitchell
Publicado 2015

Author Correction: An Autogenously Regulated Expression System for Gene Therapeutic Ocular Applications

por Sochor, Matthew A., Vasireddy, Vidyullatha, Drivas, Theodore G., Wojno, Adam, Duong, Thu T., Shpylchak, Ivan, Bennicelli, Jeannette, Chung, Daniel, Bennett, Jean, Lewis, Mitchell
Publicado 2018

AAV-Mediated Gene Therapy for Choroideremia: Preclinical Studies in Personalized Models

por Vasireddy, Vidyullatha, Mills, Jason A., Gaddameedi, Rajashekhar, Basner-Tschakarjan, Etiena, Kohnke, Monika, Black, Aaron D., Alexandrov, Krill, Zhou, Shangzhen, Maguire, Albert M., Chung, Daniel C., Mac, Helen, Sullivan, Lisa, Gadue, Paul, Bennicelli, Jeannette L., French, Deborah L., Bennett, Jean
Publicado 2013

Correction: AAV-Mediated Gene Therapy for Choroideremia: Preclinical Studies in Personalized Models

por Vasireddy, Vidyullatha, Mills, Jason A., Gaddameedi, Rajashekhar, Basner-Tschakarjan, Etiena, Kohnke, Monika, Black, Aaron D., Alexandrov, Krill, Zhou, Shangzhen, Maguire, Albert M., Chung, Daniel C., Mac, Helen, Sullivan, Lisa, Gadue, Paul, Bennicelli, Jeannette L., French, Deborah L., Bennett, Jean
Publicado 2015

Gene Therapy for Leber's Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration

por Simonelli, Francesca, Maguire, Albert M, Testa, Francesco, Pierce, Eric A, Mingozzi, Federico, Bennicelli, Jeannette L, Rossi, Settimio, Marshall, Kathleen, Banfi, Sandro, Surace, Enrico M, Sun, Junwei, Redmond, T Michael, Zhu, Xiaosong, Shindler, Kenneth S, Ying, Gui-Shuang, Ziviello, Carmela, Acerra, Carmela, Wright, J Fraser, McDonnell, Jennifer Wellman, High, Katherine A, Bennett, Jean, Auricchio, Alberto
Publicado 2009