Perspective on the Road toward Gene Therapy for Parkinson’s Disease

por Blits, Bas, Petry, Harald
Publicado 2017

Gene therapy and peripheral nerve repair: a perspective

por Hoyng, Stefan A., de Winter, Fred, Tannemaat, Martijn R., Blits, Bas, Malessy, Martijn J. A., Verhaagen, Joost
Publicado 2015

In-Depth Characterization of a Mifepristone-Regulated Expression System for AAV5-Mediated Gene Therapy in the Liver

por Liefhebber, Jolanda M., Martier, Raygene, Van der Zon, Tom, Keskin, Sonay, Huseinovic, Angelina, Lubelski, Jacek, Blits, Bas, Petry, Harald, Konstantinova, Pavlina
Publicado 2019

PhP.B Enhanced Adeno-Associated Virus Mediated-Expression Following Systemic Delivery or Direct Brain Administration

por Pietersz, Kimberly L., Plessis, Francois Du, Pouw, Stephan M., Liefhebber, Jolanda M., van Deventer, Sander J., Martens, Gerard J. M., Konstantinova, Pavlina S., Blits, Bas
Publicado 2021

Embedding siRNA sequences targeting Apolipoprotein B100 in shRNA and miRNA scaffolds results in differential processing and in vivo efficacy

por Maczuga, Piotr, Lubelski, Jacek, van Logtenstein, Richard, Borel, Florie, Blits, Bas, Fakkert, Erwin, Costessi, Adalberto, Butler, Derek, van Deventer, Sander, Petry, Harald, Koornneef, Annemart, Konstantinova, Pavlina
Publicado 2013

GFAP-Driven GFP Expression in Activated Mouse Müller Glial Cells Aligning Retinal Blood Vessels Following Intravitreal Injection of AAV2/6 Vectors

por Aartsen, Wendy M., van Cleef, Koen W. R., Pellissier, Lucie P., Hoek, Robert M., Vos, Rogier M., Blits, Bas, Ehlert, Erich M. E., Balaggan, Kamaljit S., Ali, Robin R., Verhaagen, Joost, Wijnholds, Jan
Publicado 2010

AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington’s Disease Minipig Model

por Evers, Melvin M., Miniarikova, Jana, Juhas, Stefan, Vallès, Astrid, Bohuslavova, Bozena, Juhasova, Jana, Skalnikova, Helena Kupcova, Vodicka, Petr, Valekova, Ivona, Brouwers, Cynthia, Blits, Bas, Lubelski, Jacek, Kovarova, Hana, Ellederova, Zdenka, van Deventer, Sander J., Petry, Harald, Motlik, Jan, Konstantinova, Pavlina
Publicado 2018