Cutaneous neurofibromas: patients’ medical burden, current management and therapeutic expectations: results from an online European patient community survey

por Guiraud, Marlene, Bouroubi, Athmane, Beauchamp, Roxane, Bocquet, Arnaud, Grégoire, Jean-Marc, Rauly-Lestienne, Isabelle, Blanco, Ignacio, Wolkenstein, Pierre, Schmitt, Anne-Marie
Publicado 2019

Protocol for the Phase 2 EDELIFE Trial Investigating the Efficacy and Safety of Intra-Amniotic ER004 Administration to Male Subjects with X-Linked Hypohidrotic Ectodermal Dysplasia

por Schneider, Holm, Hadj-Rabia, Smail, Faschingbauer, Florian, Bodemer, Christine, Grange, Dorothy K., Norton, Mary E., Cavalli, Riccardo, Tadini, Gianluca, Stepan, Holger, Clarke, Angus, Guillén-Navarro, Encarna, Maier-Wohlfart, Sigrun, Bouroubi, Athmane, Porte, Florence
Publicado 2023