The Group 3 Innate Lymphoid Cell Defect in Aryl Hydrocarbon Receptor Deficient Mice Is Associated with T Cell Hyperactivation during Intestinal Infection

por Wagage, Sagie, Harms Pritchard, Gretchen, Dawson, Lucas, Buza, Elizabeth L., Sonnenberg, Gregory F., Hunter, Christopher A.
Publicado 2015

Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Iduronate-2-Sulfatase in Rhesus Macaques

por Hordeaux, Juliette, Hinderer, Christian, Goode, Tamara, Buza, Elizabeth L., Bell, Peter, Calcedo, Roberto, Richman, Laura K., Wilson, James M.
Publicado 2018

Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Human Alpha-L-Iduronidase in Rhesus Macaques

por Hordeaux, Juliette, Hinderer, Christian, Goode, Tamara, Katz, Nathan, Buza, Elizabeth L., Bell, Peter, Calcedo, Roberto, Richman, Laura K., Wilson, James M.
Publicado 2018

Lipid nanoparticle-encapsulated mRNA therapy corrects serum total bilirubin level in Crigler-Najjar syndrome mouse model

por Greig, Jenny A., Chorazeczewski, Joanna K., Chowdhary, Vivek, Smith, Melanie K., Jennis, Matthew, Tarrant, James C., Buza, Elizabeth L., Coughlan, Kimberly, Martini, Paolo G.V., Wilson, James M.
Publicado 2023

Spontaneous Pancreatitis Caused by Tissue-Specific Gene Ablation of Hhex in Mice

por Ferreira, Mark J., McKenna, Lindsay B., Zhang, Jia, Reichert, Maximilian, Bakir, Basil, Buza, Elizabeth L., Furth, Emma E., Bogue, Clifford W., Rustgi, Anil K., Kaestner, Klaus H.
Publicado 2015

Determining the Minimally Effective Dose of a Clinical Candidate Adeno-Associated Virus Vector in a Mouse Model of Hemophilia A

por Greig, Jenny A., Smith, Melanie K., Nordin, Jayme M.L., Goode, Tamara, Chroscinski, Edward A., Buza, Elizabeth L., Schmidt, Nicole, Kattenhorn, Lisa M., Wadsworth, Samuel, Wilson, James M.
Publicado 2022

Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectors

por Horiuchi, Makoto, Hinderer, Christian J., Greig, Jenny A., Dyer, Cecilia, Buza, Elizabeth L., Bell, Peter, Chichester, Jessica A., Hayashi, Peter M., Yan, Hanying, Goode, Tamara, Wilson, James M.
Publicado 2022

Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectors

por Horiuchi, Makoto, Hinderer, Christian J., Greig, Jenny A., Dyer, Cecilia, Buza, Elizabeth L., Bell, Peter, Chichester, Jessica A., Hayashi, Peter M., Yan, Hanying, Goode, Tamara, Wilson, James M.
Publicado 2022

Efficacy and Safety of a Krabbe Disease Gene Therapy

por Hordeaux, Juliette, Jeffrey, Brianne A., Jian, Jinlong, Choudhury, Gourav R., Michalson, Kristofer, Mitchell, Thomas W., Buza, Elizabeth L., Chichester, Jessica, Dyer, Cecilia, Bagel, Jessica, Vite, Charles H., Bradbury, Allison M., Wilson, James M.
Publicado 2022

Immune transgene-dependent myocarditis in macaques after systemic administration of adeno-associated virus expressing human acid alpha-glucosidase

por Hordeaux, Juliette, Ramezani, Ali, Tuske, Steve, Mehta, Nickita, Song, Chunjuan, Lynch, Anna, Lupino, Katherine, Chichester, Jessica A., Buza, Elizabeth L., Dyer, Cecilia, Yu, Hongwei, Bell, Peter, Weimer, Jill M., Do, Hung, Wilson, James M.
Publicado 2023

IL-27 Limits Type 2 Immunopathology Following Parainfluenza Virus Infection

por Muallem, Gaia, Wagage, Sagie, Sun, Yan, DeLong, Jonathan H., Valenzuela, Alex, Christian, David A., Harms Pritchard, Gretchen, Fang, Qun, Buza, Elizabeth L., Jain, Deepika, Elloso, M. Merle, López, Carolina B., Hunter, Christopher A.
Publicado 2017

Prednisolone reduces the interferon response to AAV in cynomolgus macaques and may increase liver gene expression

por Wang, Lili, Warzecha, Claude C., Kistner, Alexander, Chichester, Jessica A., Bell, Peter, Buza, Elizabeth L., He, Zhenning, Pampena, M. Betina, Couthouis, Julien, Sethi, Sunjay, McKeever, Kathleen, Betts, Michael R., Kakkis, Emil, Wilson, James M., Wadsworth, Samuel, Sullivan, Barbara A.
Publicado 2022

Treating Transthyretin Amyloidosis via Adeno-Associated Virus Vector Delivery of Meganucleases

por Greig, Jenny A., Breton, Camilo, Ashley, Scott N., Martins, Kelly M., Gorsuch, Cassandra, Chorazeczewski, Joanna K., Furmanak, Thomas, Smith, Melanie K., Zhu, Yanqing, Bell, Peter, Shoop, Wendy, Li, Hui, Smith, Jeff, Tomberlin, Ginger, Clark, Peter, Mitchell, Thomas W., Buza, Elizabeth L., Yan, Hanying, Jantz, Derek, Wilson, James M.
Publicado 2022