One Size Does Not Fit All: The Past, Present and Future of Cystic Fibrosis Causal Therapies

por Ensinck, Marjolein M., Carlon, Marianne S.
Publicado 2022

On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis

por Ensinck, Marjolein, Mottais, Angélique, Detry, Claire, Leal, Teresinha, Carlon, Marianne S.
Publicado 2021

Assays of CFTR Function In Vitro, Ex Vivo and In Vivo

por Ramalho, Anabela S., Boon, Mieke, Proesmans, Marijke, Vermeulen, François, Carlon, Marianne S., De Boeck, Kris
Publicado 2022

Allele specific repair of splicing mutations in cystic fibrosis through AsCas12a genome editing

por Maule, Giulia, Casini, Antonio, Montagna, Claudia, Ramalho, Anabela S., De Boeck, Kris, Debyser, Zeger, Carlon, Marianne S., Petris, Gianluca, Cereseto, Anna
Publicado 2019

Author Correction: Allele specific repair of splicing mutations in cystic fibrosis through AsCas12a genome editing

por Maule, Giulia, Casini, Antonio, Montagna, Claudia, Ramalho, Anabela S., De Boeck, Kris, Debyser, Zeger, Carlon, Marianne S., Petris, Gianluca, Cereseto, Anna
Publicado 2020

Phenotyping of Rare CFTR Mutations Reveals Distinct Trafficking and Functional Defects

por Ensinck, Marjolein, De Keersmaecker, Liesbeth, Heylen, Lise, Ramalho, Anabela S., Gijsbers, Rik, Farré, Ricard, De Boeck, Kris, Christ, Frauke, Debyser, Zeger, Carlon, Marianne S.
Publicado 2020

Novel CFTR modulator combinations maximise rescue of G85E and N1303K in rectal organoids

por Ensinck, Marjolein M., De Keersmaecker, Liesbeth, Ramalho, Anabela S., Cuyx, Senne, Van Biervliet, Stephanie, Dupont, Lieven, Christ, Frauke, Debyser, Zeger, Vermeulen, François, Carlon, Marianne S.
Publicado 2022

Amniotic Fluid Derived Stem Cells with a Renal Progenitor Phenotype Inhibit Interstitial Fibrosis in Renal Ischemia and Reperfusion Injury in Rats

por Monteiro Carvalho Mori da Cunha, Marina Gabriela, Zia, Silvia, Oliveira Arcolino, Fanny, Carlon, Marianne Sylvia, Beckmann, Diego Vilibaldo, Pippi, Ney Luis, Luhers Graça, Dominguita, Levtchenko, Elena, Deprest, Jan, Toelen, Jaan
Publicado 2015

A Comprehensive Review on the Surgical Aspect of Lung Transplant Models in Mice and Rats

por Jin, Xin, Kaes, Janne, Van Slambrouck, Jan, Inci, Ilhan, Arni, Stephan, Geudens, Vincent, Heigl, Tobias, Jansen, Yanina, Carlon, Marianne S., Vos, Robin, Van Raemdonck, Dirk, Zhang, Yi, Vanaudenaerde, Bart M., Ceulemans, Laurens J.
Publicado 2022

Nanoblades allow high-level genome editing in murine and human organoids

por Tiroille, Victor, Krug, Adrien, Bokobza, Emma, Kahi, Michel, Bulcaen, Mattijs, Ensinck, Marjolein M., Geurts, Maarten H., Hendriks, Delilah, Vermeulen, François, Larbret, Frédéric, Gutierrez-Guerrero, Alejandra, Chen, Yu, Van Zundert, Indra, Rocha, Susana, Rios, Anne C., Medaer, Louise, Gijsbers, Rik, Mangeot, Philippe E., Clevers, Hans, Carlon, Marianne S., Bost, Frédéric, Verhoeyen, Els
Publicado 2023

Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis

por Alton, Eric W F W, Beekman, Jeffery M, Boyd, A Christopher, Brand, June, Carlon, Marianne S, Connolly, Mary M, Chan, Mario, Conlon, Sinead, Davidson, Heather E, Davies, Jane C, Davies, Lee A, Dekkers, Johanna F, Doherty, Ann, Gea-Sorli, Sabrina, Gill, Deborah R, Griesenbach, Uta, Hasegawa, Mamoru, Higgins, Tracy E, Hironaka, Takashi, Hyndman, Laura, McLachlan, Gerry, Inoue, Makoto, Hyde, Stephen C, Innes, J Alastair, Maher, Toby M, Moran, Caroline, Meng, Cuixiang, Paul-Smith, Michael C, Pringle, Ian A, Pytel, Kamila M, Rodriguez-Martinez, Andrea, Schmidt, Alexander C, Stevenson, Barbara J, Sumner-Jones, Stephanie G, Toshner, Richard, Tsugumine, Shu, Wasowicz, Marguerite W, Zhu, Jie
Publicado 2017