Hairpin end conformation of adeno-associated virus (AAV) genome determines interactions with DNA repair pathways

por Cataldi, Marcela P., McCarty, Douglas M.
Publicado 2012

Ribitol restores functionally glycosylated α-dystroglycan and improves muscle function in dystrophic FKRP-mutant mice

por Cataldi, Marcela P., Lu, Peijuan, Blaeser, Anthony, Lu, Qi Long
Publicado 2018

ISPD Overexpression Enhances Ribitol-Induced Glycosylation of α-Dystroglycan in Dystrophic FKRP Mutant Mice

por Cataldi, Marcela P., Blaeser, Anthony, Lu, Peijuan, Leroy, Victoria, Lu, Qi Long
Publicado 2019

Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery

por Fu, Haiyan, Cataldi, Marcela P, Ware, Tierra A, Zaraspe, Kimberly, Meadows, Aaron S, Murrey, Darren A, McCarty, Douglas M
Publicado 2016