Induction of long-term tolerance to a specific antigen using anti-CD3 lipid nanoparticles following gene therapy

por Chen, Chun-Yu, Vander Kooi, Amber, Cavedon, Alex, Cai, Xiaohe, Hoggatt, Jonathan, Martini, Paolo G.V., Miao, Carol H.
Publicado 2023

Treatment of Hemophilia A Using Factor VIII Messenger RNA Lipid Nanoparticles

por Chen, Chun-Yu, Tran, Dominic M., Cavedon, Alex, Cai, Xiaohe, Rajendran, Raj, Lyle, Meghan J., Martini, Paolo G.V., Miao, Carol H.
Publicado 2020

Systemic modified messenger RNA for replacement therapy in alpha 1-antitrypsin deficiency

por Karadagi, Ahmad, Cavedon, Alex G., Zemack, Helen, Nowak, Greg, Eybye, Marianne E., Zhu, Xuling, Guadagnin, Eleonora, White, Rebecca A., Rice, Lisa M., Frassetto, Andrea L., Strom, Stephen, Jorns, Carl, Martini, Paolo G. V., Ellis, Ewa
Publicado 2020