Rescue of cone function in cone-only Nphp5 knockout mouse model with Leber congenital amaurosis phenotype

por Hanke-Gogokhia, Christin, Chiodo, Vince A., Hauswirth, William W., Frederick, Jeanne M., Baehr, Wolfgang
Publicado 2018

Intraocular route of AAV2 vector administration defines humoral immune response and therapeutic potential

por Li, Qiuhong, Miller, Rehae, Han, Ping-Yang, Pang, Jijing, Dinculescu, Astra, Chiodo, Vince, Hauswirth, William W.
Publicado 2008

Next-generation sequencing of mitochondrial targeted AAV transfer of human ND4 in mice

por Yu, Hong, Mehta, Arpit, Wang, Gaofeng, Hauswirth, William W., Chiodo, Vince, Boye, Sanford L., Guy, John
Publicado 2013

Inhibitor of Apoptosis-Stimulating Protein of p53 (iASPP) Is Required for Neuronal Survival after Axonal Injury

por Wilson, Ariel M., Chiodo, Vince A., Boye, Sanford L., Brecha, Nicholas C., Hauswirth, William W., Di Polo, Adriana
Publicado 2014

Cone Phosphodiesterase-6γ’ Subunit Augments Cone PDE6 Holoenzyme Assembly and Stability in a Mouse Model Lacking Both Rod and Cone PDE6 Catalytic Subunits

por Deng, Wen-Tao, Kolandaivelu, Saravanan, Dinculescu, Astra, Li, Jie, Zhu, Ping, Chiodo, Vince A., Ramamurthy, Visvanathan, Hauswirth, William W.
Publicado 2018

rAAV2/5 gene-targeting to rods: dose-dependent efficiency and complications associated with different promoters

por Beltran, William A., Boye, Sanford L., Boye, Shannon E., Chiodo, Vince A., Lewin, Alfred S., Hauswirth, William W., Aguirre, Gustavo D.
Publicado 2010

AAV2-Mediated Expression of HspB1 in RGCs Prevents Somal Damage and Axonal Transport Deficits in a Mouse Model of Ocular Hypertension

por Nam, Mi-Hyun, Nahomi, Rooban B., Pantcheva, Mina B., Dhillon, Armaan, Chiodo, Vince A., Smith, W. Clay, Nagaraj, Ram H.
Publicado 2022

Retinal gene therapy with a large MYO7A cDNA using adeno-associated virus

por Lopes, Vanda S., Boye, Shannon E., Louie, Carrie M., Boye, Sanford, Dyka, Frank, Chiodo, Vince, Fofo, Hugo, Hauswirth, William W., Williams, David S.
Publicado 2013

Human L- and M-opsins restore M-cone function in a mouse model for human blue cone monochromacy

por Deng, Wen-Tao, Li, Jie, Zhu, Ping, Chiodo, Vince A., Smith, W. Clay, Freedman, Beau, Baehr, Wolfgang, Pang, Jijing, Hauswirth, William W.
Publicado 2018

Mutant NADH dehydrogenase subunit 4 gene delivery to mitochondria by targeting sequence-modified adeno-associated virus induces visual loss and optic atrophy in mice

por Yu, Hong, Ozdemir, Sacide S., Koilkonda, Rajeshwari D., Chou, Tsung-Han, Porciatti, Vittorio, Chiodo, Vince, Boye, Sanford L., Hauswirth, William W., Lewin, Alfred S., Guy, John
Publicado 2012

Transgene expression of Stanniocalcin-1 provides sustained intraocular pressure reduction by increasing outflow facility

por Roddy, Gavin W., Roy Chowdhury, Uttio, Anderson, Kjersten J., Rinkoski, Tommy A., Hann, Cheryl R., Chiodo, Vince A., Smith, W. Clay, Fautsch, Michael P.
Publicado 2022

In vivo knockdown of Piccolino disrupts presynaptic ribbon morphology in mouse photoreceptor synapses

por Regus-Leidig, Hanna, Fuchs, Michaela, Löhner, Martina, Leist, Sarah R., Leal-Ortiz, Sergio, Chiodo, Vince A., Hauswirth, William W., Garner, Craig C., Brandstätter, Johann H.
Publicado 2014

Intravitreal Administration of AAV2-SIRT1 Reverses Diabetic Retinopathy in a Mouse Model of Type 2 Diabetes

por Adu-Agyeiwaah, Yvonne, Vieira, Cristiano P., Asare-Bediako, Bright, Li Calzi, Sergio, DuPont, Mariana, Floyd, Jason, Boye, Sanford, Chiodo, Vince, Busik, Julia V., Grant, Maria B.
Publicado 2023

Neuroprotective Gene Therapy by Overexpression of the Transcription Factor MAX in Rat Models of Glaucomatous Neurodegeneration

por Lani-Louzada, Rafael, Marra, Camila, Dias, Mariana Santana, de Araújo, Victor Guedes, Abreu, Carla Andreia, Ribas, Vinícius Toledo, Adesse, Daniel, Allodi, Silvana, Chiodo, Vince, Hauswirth, William, Petrs-Silva, Hilda, Linden, Rafael
Publicado 2022

AAV-Mediated Cone Rescue in a Naturally Occurring Mouse Model of CNGA3-Achromatopsia

por Pang, Ji-jing, Deng, Wen-Tao, Dai, Xufeng, Lei, Bo, Everhart, Drew, Umino, Yumiko, Li, Jie, Zhang, Keqing, Mao, Song, Boye, Sanford L., Liu, Li, Chiodo, Vince A., Liu, Xuan, Shi, Wei, Tao, Ye, Chang, Bo, Hauswirth, William W.
Publicado 2012

Correction: AAV-Mediated Cone Rescue in a Naturally Occurring Mouse Model of CNGA3-Achromatopsia

por Pang, Ji-jing, Deng, Wen-Tao, Dai, Xufeng, Lei, Bo, Everhart, Drew, Umino, Yumiko, Li, Jie, Zhang, Keqing, Mao, Song, Boye, Sanford L., Liu, Li, Chiodo, Vince A., Liu, Xuan, Shi, Wei, Tao, Ye, Chang, Bo, Hauswirth, William W.
Publicado 2014

BEST1 gene therapy corrects a diffuse retina-wide microdetachment modulated by light exposure

por Guziewicz, Karina E., Cideciyan, Artur V., Beltran, William A., Komáromy, András M., Dufour, Valerie L., Swider, Malgorzata, Iwabe, Simone, Sumaroka, Alexander, Kendrick, Brian T., Ruthel, Gordon, Chiodo, Vince A., Héon, Elise, Hauswirth, William W., Jacobson, Samuel G., Aguirre, Gustavo D.
Publicado 2018

AAV-Mediated Clarin-1 Expression in the Mouse Retina: Implications for USH3A Gene Therapy

por Dinculescu, Astra, Stupay, Rachel M., Deng, Wen-Tao, Dyka, Frank M., Min, Seok-Hong, Boye, Sanford L., Chiodo, Vince A., Abrahan, Carolina E., Zhu, Ping, Li, Qiuhong, Strettoi, Enrica, Novelli, Elena, Nagel-Wolfrum, Kerstin, Wolfrum, Uwe, Smith, W. Clay, Hauswirth, William W.
Publicado 2016

Patients and animal models of CNGβ1-deficient retinitis pigmentosa support gene augmentation approach

por Petersen-Jones, Simon M., Occelli, Laurence M., Winkler, Paige A., Lee, Winston, Sparrow, Janet R., Tsukikawa, Mai, Boye, Sanford L., Chiodo, Vince, Capasso, Jenina E., Becirovic, Elvir, Schön, Christian, Seeliger, Mathias W., Levin, Alex V., Michalakis, Stylianos, Hauswirth, William W., Tsang, Stephen H.
Publicado 2017

Photoreceptor avascular privilege is shielded by soluble VEGF receptor-1

por Luo, Ling, Uehara, Hironori, Zhang, Xiaohui, Das, Subrata K, Olsen, Thomas, Holt, Derick, Simonis, Jacquelyn M, Jackman, Kyle, Singh, Nirbhai, Miya, Tadashi R, Huang, Wei, Ahmed, Faisal, Bastos-Carvalho, Ana, Le, Yun Zheng, Mamalis, Christina, Chiodo, Vince A, Hauswirth, William W, Baffi, Judit, Lacal, Pedro M, Orecchia, Angela, Ferrara, Napoleone, Gao, Guangping, Young-hee, Kim, Fu, Yingbin, Owen, Leah, Albuquerque, Romulo, Baehr, Wolfgang, Thomas, Kirk, Li, Dean Y, Chalam, Kakarla V, Shibuya, Masabumi, Grisanti, Salvatore, Wilson, David J, Ambati, Jayakrishna, Ambati, Balamurali K
Publicado 2013