Development of a one-step RT-ddPCR method to determine the expression and potency of AAV vectors

por Clarner, Pete, Lau, Shukkwan K., Chowdhury, Twinkle, Guilmette, Edward, Trapa, Patrick, Lo, Shih-Ching, Shen, Shen
Publicado 2021

Development and Application of a Liquid Chromatography-Mass Spectrometry Method for Residual Iodixanol Quantification in AAV-Based Gene Therapy Product Development

por Pu, Yi, Katz, Russell, Chen, Yunqiu, Kostrubsky, Vic, Clarner, Pete, Lo, Shih-Ching, Sosic, Zoran, Yeung, Bernice
Publicado 2022

Efficacy and safety of a SOD1-targeting artificial miRNA delivered by AAV9 in mice are impacted by miRNA scaffold selection

por Chen, Shukkwan K., Hawley, Zachary C.E., Zavodszky, Maria I., Hana, Sam, Ferretti, Daniel, Grubor, Branka, Hawes, Michael, Xu, Shanqin, Hamann, Stefan, Marsh, Galina, Cullen, Patrick, Challa, Ravi, Carlile, Thomas M., Zhang, Hang, Lee, Wan-Hung, Peralta, Andrea, Clarner, Pete, Wei, Cong, Koszka, Kathryn, Gao, Feng, Lo, Shih-Ching
Publicado 2023