Core data set on safety, efficacy, and durability of hemophilia gene therapy for a global registry: Communication from the SSC of the ISTH

por Konkle, Barbara, Pierce, Glen, Coffin, Donna, Naccache, Mayss, Clark, R. Cary, George, Lindsey, Iorio, Alfonso, O’Mahony, Brian, Pipe, Steven, Skinner, Mark, Watson, Crystal, Peyvandi, Flora, Mahlangu, Johnny
Publicado 2020

Patient‐relevant health outcomes for hemophilia care: Development of an international standard outcomes set

por van Balen, Erna C., O'Mahony, Brian, Cnossen, Marjon H., Dolan, Gerard, Blanchette, Victor S., Fischer, Kathelijn, Gue, Deborah, O'Hara, Jamie, Iorio, Alfonso, Jackson, Shannon, Konkle, Barbara A., Nugent, Diane J., Coffin, Donna, Skinner, Mark W., Smit, Cees, Srivastava, Alok, van Eenennaam, Fred, van der Bom, Johanna G., Gouw, Samantha C.
Publicado 2021