Gene therapy in the putamen for curing AADC deficiency and Parkinson's disease

por Hwu, Paul Wuh‐Liang, Kiening, Karl, Anselm, Irina, Compton, David R, Nakajima, Takeshi, Opladen, Thomas, Pearl, Phillip L, Roubertie, Agathe, Roujeau, Thomas, Muramatsu, Shin‐ichi
Publicado 2021

Nonclinical Studies that Support Viral Vector-Delivered Gene Therapies: An EFPIA Gene Therapy Working Group Perspective

por Bolt, Michael W., Whiteley, Laurence O., Lynch, Jessica L., Lauritzen, Brian, Fernández de Henestrosa, Antonio R., MacLachlan, Timothy, Ulrich, Peter, Philip, Binu K., Mahalingaiah, Prathap Kumar, Fuller, Claudette L., Compton, David R.
Publicado 2020