Cystic fibrosis presenting as recurrent pancreatitis in a young child with a normal sweat test and pancreas divisum: a case report

por Conklin, Laurie, Zeitlin, Pamela L, Cuffari, Carmen
Publicado 2008

Serum biomarkers associated with baseline clinical severity in young steroid-naïve Duchenne muscular dystrophy boys

por Dang, Utkarsh J, Ziemba, Michael, Clemens, Paula R, Hathout, Yetrib, Conklin, Laurie S, Hoffman, Eric P
Publicado 2020

The Role of Master Protocols in Pediatric Drug Development

por Nelson, Robert M., Conklin, Laurie S., Komocsar, Wendy J., Chen, Fei, Williamson, Forrest, Crandall, Wallace V.
Publicado 2022

Identification of Pathway-Specific Serum Biomarkers of Response to Glucocorticoid and Infliximab Treatment in Children with Inflammatory Bowel Disease

por Heier, Christopher R, Fiorillo, Alyson A, Chaisson, Ellen, Gordish-Dressman, Heather, Hathout, Yetrib, Damsker, Jesse M, Hoffman, Eric P, Conklin, Laurie S
Publicado 2016

Serum miRNAs Are Pharmacodynamic Biomarkers Associated With Therapeutic Response in Pediatric Inflammatory Bowel Disease

por Batra, Suruchi K, Heier, Christopher R, Diaz-Calderon, Lina, Tully, Christopher B, Fiorillo, Alyson A, van den Anker, John, Conklin, Laurie S
Publicado 2020

Validating the Simplified Endoscopic Mucosal Assessment for Crohn’s Disease: A Novel Method for Assessing Disease Activity

por Adler, Jeremy, Colletti, Richard B, Noonan, Lenore, Berzin, Tyler M, Cheifetz, Adam S, Conklin, Laurie S, Hoops, Timothy C, Huang, Christopher S, Lewis, Blair, Mishkin, Daniel S, Hung Lo, Kim, Xiao, Yongling, Volger, Sheri
Publicado 2022

Using multiple imputation of real-world data to estimate clinical remission in pediatric inflammatory bowel disease

por Zhang, Nanhua, Liu, Chunyan, Steiner, Steven J, Colletti, Richard B, Baldassano, Robert, Chen, Shiran, Cohen, Stanley, Kappelman, Michael D, Saeed, Shehzad, Conklin, Laurie S, Strauss, Richard, Volger, Sheri, King, Eileen, Lo, Kim Hung
Publicado 2023

Innovations in Pediatric Therapeutics Development: Principles for the Use of Bridging Biomarkers in Pediatric Extrapolation

por Fleming, Thomas R., Garnett, Christine E., Conklin, Laurie S., Corriol-Rohou, Solange, Hariharan, Sudharshan, Hsu, Daphne, Mueller-Velten, Guenther, Mulugeta, Yeruk, Portman, Ronald, Rothmann, Mark D., Stockbridge, Norman L., Wandel, Simon, Zhang, Jialu, Yao, Lynne
Publicado 2022

Disease-specific and glucocorticoid-responsive serum biomarkers for Duchenne Muscular Dystrophy

por Hathout, Yetrib, Liang, Chen, Ogundele, Michael, Xu, Ganggang, Tawalbeh, Shefa M., Dang, Utkarsh J, Hoffman, Eric P., Gordish-Dressman, Heather, Conklin, Laurie S., van den Anker, John N., Clemens, Paula R., Mah, Jean K., Henricson, Erik, McDonald, Craig
Publicado 2019

Serum biomarkers of glucocorticoid response and safety in anti-neutrophil cytoplasmic antibody-associated vasculitis and juvenile dermatomyositis

por Conklin, Laurie S., Merkel, Peter A., Pachman, Lauren M., Parikh, Hemang, Tawalbeh, Shefa, Damsker, Jesse M., Cuthbertson, David D., Morgan, Gabrielle A., Monach, Paul A., Hathout, Yetrib, Nagaraju, Kanneboyina, van den Anker, John, McAlear, Carol A., Hoffman, Eric P.
Publicado 2018

Towards the international interoperability of clinical research networks for rare diseases: recommendations from the IRDiRC Task Force

por Nabbout, Rima, Zanello, Galliano, Baker, Dixie, Black, Lora, Brambilla, Isabella, Buske, Orion J., Conklin, Laurie S., Davies, Elin Haf, Julkowska, Daria, Kim, Yeonju, Klopstock, Thomas, Nakamura, Harumasa, Nielsen, Kim G., Pariser, Anne R., Pastor, Jose Carlos, Scarpa, Maurizio, Smith, Maureen, Taruscio, Domenica, Groft, Stephen
Publicado 2023

Serum pharmacodynamic biomarkers for chronic corticosteroid treatment of children

por Hathout, Yetrib, Conklin, Laurie S., Seol, Haeri, Gordish-Dressman, Heather, Brown, Kristy J., Morgenroth, Lauren P., Nagaraju, Kanneboyina, Heier, Christopher R., Damsker, Jesse M., van den Anker, John N., Henricson, Erik, Clemens, Paula R., Mah, Jean K., McDonald, Craig, Hoffman, Eric P.
Publicado 2016

Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study

por Smith, Edward C., Conklin, Laurie S., Hoffman, Eric P., Clemens, Paula R., Mah, Jean K., Finkel, Richard S., Guglieri, Michela, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M., Webster, Richard, Castro, Diana, Kuntz, Nancy L., Kerchner, Laurie, Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Jaros, Mark, Shale, Phil, Gordish-Dressman, Heather, Hagerty, Laura, Dang, Utkarsh J., Damsker, Jesse M., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., McDonald, Craig M.
Publicado 2020

Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function

por Hoffman, Eric P., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., Smith, Edward C., Castro, Diana, Mah, Jean K., McDonald, Craig M., Kuntz, Nancy L., Finkel, Richard S., Guglieri, Michela, Bushby, Katharine, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M., Webster, Richard, Smith, Andrea L., Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Siener, Catherine, Jaros, Mark, Shale, Phil, McCall, John M., Nagaraju, Kanneboyina, van den Anker, John, Conklin, Laurie S., Cnaan, Avital, Gordish-Dressman, Heather, Damsker, Jesse M., Clemens, Paula R.
Publicado 2019