mRNA treatment produces sustained expression of enzymatically active human ADAMTS13 in mice

por Liu-Chen, Susan, Connolly, Brendan, Cheng, Lei, Subramanian, Romesh R., Han, Zhaozhong
Publicado 2018

SERPINA1 mRNA as a Treatment for Alpha-1 Antitrypsin Deficiency

por Connolly, Brendan, Isaacs, Cleo, Cheng, Lei, Asrani, Kirtika H., Subramanian, Romesh R.
Publicado 2018