Ganglioside GM3 Levels Are Altered in a Mouse Model of HIBM: GM3 as a Cellular Marker of the Disease

por Paccalet, Thomas, Coulombe, Zoé, Tremblay, Jacques P.
Publicado 2010

A Potential New Therapeutic Approach for Friedreich Ataxia: Induction of Frataxin Expression With TALE Proteins

por Chapdelaine, Pierre, Coulombe, Zoé, Chikh, Amina, Gérard, Catherine, Tremblay, Jacques P
Publicado 2013

An AAV9 coding for frataxin clearly improved the symptoms and prolonged the life of Friedreich ataxia mouse models

por Gérard, Catherine, Xiao, Xiao, Filali, Mohammed, Coulombe, Zoé, Arsenault, Marie, Couet, Jacques, Li, Juan, Drolet, Marie-Claude, Chapdelaine, Pierre, Chikh, Amina, Tremblay, Jacques P
Publicado 2014