CRISPR/Cas9-Mediated Correction of the FANCD1 Gene in Primary Patient Cells

por Skvarova Kramarzova, Karolina, Osborn, Mark J., Webber, Beau R., DeFeo, Anthony P., McElroy, Amber N., Kim, Chong Jai, Tolar, Jakub
Publicado 2017

CRISPR/Cas9-based genetic correction for recessive dystrophic epidermolysis bullosa

por Webber, Beau R, Osborn, Mark J, McElroy, Amber N, Twaroski, Kirk, Lonetree, Cara-lin, DeFeo, Anthony P, Xia, Lily, Eide, Cindy, Lees, Christopher J, McElmurry, Ron T, Riddle, Megan J, Kim, Chong Jai, Patel, Dharmeshkumar D, Blazar, Bruce R, Tolar, Jakub
Publicado 2016

Correction of Fanconi Anemia Mutations Using Digital Genome Engineering

por Sipe, Christopher J., Kluesner, Mitchell G., Bingea, Samuel P., Lahr, Walker S., Andrew, Aneesha A., Wang, Minjing, DeFeo, Anthony P., Hinkel, Timothy L., Laoharawee, Kanut, Wagner, John E., MacMillan, Margaret L., Vercellotti, Gregory M., Tolar, Jakub, Osborn, Mark J., McIvor, R. Scott, Webber, Beau R., Moriarity, Branden S.
Publicado 2022