Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy

por Duan, Dongsheng
Publicado 2018

Marginal Level Dystrophin Expression Improves Clinical Outcome in a Strain of Dystrophin/Utrophin Double Knockout Mice

por Li, Dejia, Yue, Yongping, Duan, Dongsheng
Publicado 2010

iNOS Ablation Does Not Improve Specific Force of the Extensor Digitorum Longus Muscle in Dystrophin-Deficient mdx4cv Mice

por Li, Dejia, Shin, Jin-Hong, Duan, Dongsheng
Publicado 2011

CRISPR-Cas9 cleavage efficiency correlates strongly with target-sgRNA folding stability: from physical mechanism to off-target assessment

por Xu, Xiaojun, Duan, Dongsheng, Chen, Shi-Jie
Publicado 2017

Evaluation of Muscle Function of the Extensor Digitorum Longus Muscle Ex vivo and Tibialis Anterior Muscle In situ in Mice

por Hakim, Chady H., Wasala, Nalinda B., Duan, Dongsheng
Publicado 2013

100-fold but not 50-fold dystrophin overexpression aggravates electrocardiographic defects in the mdx model of Duchenne muscular dystrophy

por Yue, Yongping, Wasala, Nalinda B, Bostick, Brian, Duan, Dongsheng
Publicado 2016

Editorial: Genome and transcriptome editing to understand and treat neuromuscular diseases

por Maruyama, Rika, Fiorillo, Alyson, Heier, Christopher, Duan, Dongsheng, Yokota, Toshifumi
Publicado 2023

Adeno-associated virus serotype-9 efficiently transduces the retinal outer plexiform layer

por Lei, Bo, Zhang, Keqing, Yue, Yongping, Ghosh, Arkasubhra, Duan, Dongsheng
Publicado 2009

Manipulation of mtDNA heteroplasmy in all striated muscles of newborn mice by AAV9-mediated delivery of a mitochondria targeted restriction endonuclease

por Bacman, Sandra R., Williams, Sion L., Duan, Dongsheng, Moraes, Carlos T.
Publicado 2011

Abnormal Calcium Handling in Duchenne Muscular Dystrophy: Mechanisms and Potential Therapies

por Mareedu, Satvik, Million, Emily D., Duan, Dongsheng, Babu, Gopal J.
Publicado 2021

SERCA2a gene transfer improves electrocardiographic performance in aged mdx mice

por Shin, Jin-Hong, Bostick, Brian, Yue, Yongping, Hajjar, Roger, Duan, Dongsheng
Publicado 2011

Ectopic Catalase Expression in Mitochondria by Adeno-Associated Virus Enhances Exercise Performance in Mice

por Li, Dejia, Lai, Yi, Yue, Yongping, Rabinovitch, Peter S., Hakim, Chady, Duan, Dongsheng
Publicado 2009

Night Activity Reduction is a Signature Physiological Biomarker for Duchenne Muscular Dystrophy Dogs

por Hakim, Chady H., Peters, Austin A., Feng, Feng, Yao, Gang, Duan, Dongsheng
Publicado 2015

Dystrophin R16/17-syntrophin PDZ fusion protein restores sarcolemmal nNOSμ

por Patel, Aman, Zhao, Junling, Yue, Yongping, Zhang, Keqing, Duan, Dongsheng, Lai, Yi
Publicado 2018

Four-limb wireless IMU sensor system for automatic gait detection in canines

por Zhang, Xiqiao, Jenkins, Gregory J., Hakim, Chady H., Duan, Dongsheng, Yao, Gang
Publicado 2022

The FVB Background Does Not Dramatically Alter the Dystrophic Phenotype of Mdx Mice

por Wasala, Nalinda B., Zhang, Keqing, Wasala, Lakmini P., Hakim, Chady H., Duan, Dongsheng
Publicado 2015

Animal models of Duchenne muscular dystrophy: from basic mechanisms to gene therapy

por McGreevy, Joe W., Hakim, Chady H., McIntosh, Mark A., Duan, Dongsheng
Publicado 2015

Automatic characterization of stride parameters in canines with a single wearable inertial sensor

por Jenkins, Gregory J., Hakim, Chady H., Yang, N. Nora, Yao, Gang, Duan, Dongsheng
Publicado 2018

Development of capsid- and genome-modified optimized AAVrh74 vectors for muscle gene therapy

por Shoti, Jakob, Qing, Keyun, Keeler, Geoffrey D., Duan, Dongsheng, Byrne, Barry J., Srivastava, Arun
Publicado 2023

Early loss of ambulation is not a representative clinical feature in Duchenne muscular dystrophy dogs: remarks on the article of Barthélémy et al.

por Duan, Dongsheng, Hakim, Chady H., Ambrosio, Carlos E., Smith, Bruce F., Sweeney, H. Lee
Publicado 2015