miRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3

por Nobre, Rui Jorge, Lobo, Diana D., Henriques, Carina, Duarte, Sonia P., Lopes, Sara M., Silva, Ana C., Lopes, Miguel M., Mariet, Fanny, Schwarz, Lukas K., Baatje, M.S., Ferreira, Valerie, Vallès, Astrid, Pereira de Almeida, Luis, Evers, Melvin M., Toonen, Lodewijk J.A.
Publicado 2022