One Size Does Not Fit All: The Past, Present and Future of Cystic Fibrosis Causal Therapies

por Ensinck, Marjolein M., Carlon, Marianne S.
Publicado 2022

On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis

por Ensinck, Marjolein, Mottais, Angélique, Detry, Claire, Leal, Teresinha, Carlon, Marianne S.
Publicado 2021

Phenotyping of Rare CFTR Mutations Reveals Distinct Trafficking and Functional Defects

por Ensinck, Marjolein, De Keersmaecker, Liesbeth, Heylen, Lise, Ramalho, Anabela S., Gijsbers, Rik, Farré, Ricard, De Boeck, Kris, Christ, Frauke, Debyser, Zeger, Carlon, Marianne S.
Publicado 2020

Novel CFTR modulator combinations maximise rescue of G85E and N1303K in rectal organoids

por Ensinck, Marjolein M., De Keersmaecker, Liesbeth, Ramalho, Anabela S., Cuyx, Senne, Van Biervliet, Stephanie, Dupont, Lieven, Christ, Frauke, Debyser, Zeger, Vermeulen, François, Carlon, Marianne S.
Publicado 2022

Nanoblades allow high-level genome editing in murine and human organoids

por Tiroille, Victor, Krug, Adrien, Bokobza, Emma, Kahi, Michel, Bulcaen, Mattijs, Ensinck, Marjolein M., Geurts, Maarten H., Hendriks, Delilah, Vermeulen, François, Larbret, Frédéric, Gutierrez-Guerrero, Alejandra, Chen, Yu, Van Zundert, Indra, Rocha, Susana, Rios, Anne C., Medaer, Louise, Gijsbers, Rik, Mangeot, Philippe E., Clevers, Hans, Carlon, Marianne S., Bost, Frédéric, Verhoeyen, Els
Publicado 2023