CRISPR Therapeutics for Duchenne Muscular Dystrophy

por Erkut, Esra, Yokota, Toshifumi
Publicado 2022

DG9-conjugated morpholino rescues phenotype in SMA mice by reaching the CNS via a subcutaneous administration

por Aslesh, Tejal, Erkut, Esra, Ren, Jun, Lim, Kenji Rowel Q., Woo, Stanley, Hatlevig, Susan, Moulton, Hong M., Gosgnach, Simon, Greer, John, Maruyama, Rika, Yokota, Toshifumi
Publicado 2023

In vitro maturation and in vivo stability of bioprinted human nasal cartilage

por Lan, Xiaoyi, Liang, Yan, Vyhlidal, Margaret, Erkut, Esra JN, Kunze, Melanie, Mulet-Sierra, Aillette, Osswald, Martin, Ansari, Khalid, Seikaly, Hadi, Boluk, Yaman, Adesida, Adetola B
Publicado 2022

eSkip-Finder: a machine learning-based web application and database to identify the optimal sequences of antisense oligonucleotides for exon skipping

por Chiba, Shuntaro, Lim, Kenji Rowel Q, Sheri, Narin, Anwar, Saeed, Erkut, Esra, Shah, Md Nur Ahad, Aslesh, Tejal, Woo, Stanley, Sheikh, Omar, Maruyama, Rika, Takano, Hiroaki, Kunitake, Katsuhiko, Duddy, William, Okuno, Yasushi, Aoki, Yoshitsugu, Yokota, Toshifumi
Publicado 2021