Liposomes to Target Peripheral Neurons and Schwann Cells

por Lee, Sooyeon, Ashizawa, Ana Tari, Kim, Kwang Sik, Falk, Darin J., Notterpek, Lucia
Publicado 2013

A scalable method for the production of high-titer and high-quality adeno-associated type 9 vectors using the HSV platform

por Adamson-Small, Laura, Potter, Mark, Falk, Darin J, Cleaver, Brian, Byrne, Barry J, Clément, Nathalie
Publicado 2016

(13)C/(31)P MRS Metabolic Biomarkers of Disease Progression and Response to AAV Delivery of hGAA in a Mouse Model of Pompe Disease

por Baligand, Celine, Todd, Adrian G., Lee-McMullen, Brittany, Vohra, Ravneet S., Byrne, Barry J., Falk, Darin J., Walter, Glenn A.
Publicado 2017

Comparative impact of AAV and enzyme replacement therapy on respiratory and cardiac function in adult Pompe mice

por Falk, Darin J, Soustek, Meghan S, Todd, Adrian Gary, Mah, Cathryn S, Cloutier, Denise A, Kelley, Jeffry S, Clement, Nathalie, Fuller, David D, Byrne, Barry J
Publicado 2015

Hypoglossal Neuropathology and Respiratory Activity in Pompe Mice

por Lee, Kun-Ze, Qiu, Kai, Sandhu, Milapjit S., Elmallah, Mai K., Falk, Darin J., Lane, Michael A., Reier, Paul J., Byrne, Barry J., Fuller, David D.
Publicado 2011

AAV Gene Therapy Utilizing Glycosylation-Independent Lysosomal Targeting Tagged GAA in the Hypoglossal Motor System of Pompe Mice

por Doyle, Brendan M., Turner, Sara M.F., Sunshine, Michael D., Doerfler, Phillip A., Poirier, Amy E., Vaught, Lauren A., Jorgensen, Marda L., Falk, Darin J., Byrne, Barry J., Fuller, David D.
Publicado 2019

An acidic oligopeptide displayed on AAV2 improves axial muscle tropism after systemic delivery

por Lee, Ni-Chung, Falk, Darin J, Byrne, Barry J, Conlon, Thomas J, Clement, Nathalie, Porvasnik, Stacy, Jorgensen, Marda L, Potter, Mark, Erger, Kirsten E, Watson, Rachael, Ghivizzani, Steven C, Chiu, Hung-Chuan, Chien, Yin-Hsiu, Hwu, Wuh-Liang
Publicado 2012