Comparisons Between Separately Conducted Clinical Trials: Letter to the Editor Regarding Dabbous O, Maru B, Jansen JP, Lorenzi M, Cloutier M, Guérin A, et al. Adv Ther (2019) 36(5)...

por Sandrock, Alfred W., Farwell, Wildon
Publicado 2019

Lack of Cholesterol Awareness among Physicians Who Smoke

por Scranton, Richard E., Farwell, Wildon R., Gaziano, John M.
Publicado 2009

Indirect estimation of the prevalence of spinal muscular atrophy Type I, II, and III in the United States

por Lally, Cathy, Jones, Cynthia, Farwell, Wildon, Reyna, Sandra P., Cook, Suzanne F., Flanders, W. Dana
Publicado 2017

Pharmacokinetics of renally excreted drug dexpramipexole in subjects with impaired renal function

por He, Ping, Kerr, Doug, Marbury, Thomas, Ries, Daniel, Farwell, Wildon, Stecher, Scott, Dong, Yingwen, Wei, Dong, Rogge, Mark
Publicado 2014

Spinal Muscular Atrophy (SMA) Subtype Concordance in Siblings: Findings From the Cure SMA Cohort

por Jones, Cynthia C., Cook, Suzanne F., Jarecki, Jill, Belter, Lisa, Reyna, Sandra P., Staropoli, John, Farwell, Wildon, Hobby, Kenneth
Publicado 2020

An Integrated Safety Analysis of Infants and Children with Symptomatic Spinal Muscular Atrophy (SMA) Treated with Nusinersen in Seven Clinical Trials

por Darras, Basil T., Farrar, Michelle A., Mercuri, Eugenio, Finkel, Richard S., Foster, Richard, Hughes, Steven G., Bhan, Ishir, Farwell, Wildon, Gheuens, Sarah
Publicado 2019

Position Statement: Sharing of Clinical Research Data in Spinal Muscular Atrophy to Accelerate Research and Improve Outcomes for Patients

por Lochmüller, Hanns, Evans, David, Farwell, Wildon, Finkel, Richard, Goemans, Nathalie, de Lemus, Mencia, Matyushenko, Vitaliy, Muntoni, Francesco, Ouillade, Marie-Christine, Schwersenz, Inge, Wilson, Petra
Publicado 2018

Increased systemic HSP70B levels in spinal muscular atrophy infants

por Eichelberger, Eric J., Alves, Christiano R. R., Zhang, Ren, Petrillo, Marco, Cullen, Patrick, Farwell, Wildon, Hurt, Jessica A., Staropoli, John F., Swoboda, Kathryn J.
Publicado 2021

Safety and efficacy of nusinersen in spinal muscular atrophy: The EMBRACE study

por Acsadi, Gyula, Crawford, Thomas O., Müller‐Felber, Wolfgang, Shieh, Perry B., Richardson, Randal, Natarajan, Niranjana, Castro, Diana, Ramirez‐Schrempp, Daniela, Gambino, Giulia, Sun, Peng, Farwell, Wildon
Publicado 2021

Comparative All-Cause Mortality Among a Large Population of Patients with Spinal Muscular Atrophy Versus Matched Controls

por Viscidi, Emma, Juneja, Maneesh, Wang, Jin, Wang, Nasha, Li, Li, Farwell, Wildon, Bhan, Ishir, Makepeace, Corinne, Laird, Karen, Kupelian, Varant, Eaton, Susan, Dilley, Anne, Hall, Susan
Publicado 2021

Correction to: Comparative All-Cause Mortality Among a Large Population of Patients with Spinal Muscular Atrophy Versus Matched Controls

por Viscidi, Emma, Juneja, Maneesh, Wang, Jin, Wang, Nasha, Li, Li, Farwell, Wildon, Bhan, Ishir, Makepeace, Corinne, Laird, Karen, Kupelian, Varant, Eaton, Susan, Dilley, Anne, Hall, Susan
Publicado 2022

Identifying Biomarkers of Spinal Muscular Atrophy for Further Development

por Glascock, Jacqueline, Darras, Basil T., Crawford, Thomas O., Sumner, Charlotte J., Kolb, Stephen J., DiDonato, Christine, Elsheikh, Bakri, Howell, Kelly, Farwell, Wildon, Valente, Marta, Petrillo, Marco, Tingey, Jessica, Jarecki, Jill
Publicado 2023

Implications of circulating neurofilaments for spinal muscular atrophy treatment early in life: A case series

por Alves, Christiano R.R., Petrillo, Marco, Spellman, Rebecca, Garner, Reid, Zhang, Ren, Kiefer, Michael, Simeone, Sarah, Sohn, Jihee, Eichelberger, Eric J., Rodrigues, Emma, Arruda, Elizabeth A., Townsend, Elise L., Farwell, Wildon, Swoboda, Kathryn J.
Publicado 2021

Nusinersen improves walking distance and reduces fatigue in later‐onset spinal muscular atrophy

por Montes, Jacqueline, Dunaway Young, Sally, Mazzone, Elena S., Pasternak, Amy, Glanzman, Allan M., Finkel, Richard S., Darras, Basil T., Muntoni, Francesco, Mercuri, Eugenio, De Vivo, Darryl C., Bishop, Kathie M., Schneider, Eugene, Bennett, C. Frank, Foster, Richard, Farwell, Wildon
Publicado 2019

Neurofilament as a potential biomarker for spinal muscular atrophy

por Darras, Basil T., Crawford, Thomas O., Finkel, Richard S., Mercuri, Eugenio, De Vivo, Darryl C., Oskoui, Maryam, Tizzano, Eduardo F., Ryan, Monique M., Muntoni, Francesco, Zhao, Guolin, Staropoli, John, McCampbell, Alexander, Petrillo, Marco, Stebbins, Christopher, Fradette, Stephanie, Farwell, Wildon, Sumner, Charlotte J.
Publicado 2019

Nusinersen in later-onset spinal muscular atrophy: Long-term results from the phase 1/2 studies

por Darras, Basil T., Chiriboga, Claudia A., Iannaccone, Susan T., Swoboda, Kathryn J., Montes, Jacqueline, Mignon, Laurence, Xia, Shuting, Bennett, C. Frank, Bishop, Kathie M., Shefner, Jeremy M., Green, Allison M., Sun, Peng, Bhan, Ishir, Gheuens, Sarah, Schneider, Eugene, Farwell, Wildon, De Vivo, Darryl C.
Publicado 2019

Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study

por De Vivo, Darryl C., Bertini, Enrico, Swoboda, Kathryn J., Hwu, Wuh-Liang, Crawford, Thomas O., Finkel, Richard S., Kirschner, Janbernd, Kuntz, Nancy L., Parsons, Julie A., Ryan, Monique M., Butterfield, Russell J., Topaloglu, Haluk, Ben-Omran, Tawfeg, Sansone, Valeria A., Jong, Yuh-Jyh, Shu, Francy, Staropoli, John F., Kerr, Douglas, Sandrock, Alfred W., Stebbins, Christopher, Petrillo, Marco, Braley, Gabriel, Johnson, Kristina, Foster, Richard, Gheuens, Sarah, Bhan, Ishir, Reyna, Sandra P., Fradette, Stephanie, Farwell, Wildon
Publicado 2019