TALEN-Mediated Gene Editing of HBG in Human Hematopoietic Stem Cells Leads to Therapeutic Fetal Hemoglobin Induction

por Lux, Christopher T., Pattabhi, Sowmya, Berger, Mason, Nourigat, Cynthia, Flowers, David A., Negre, Olivier, Humbert, Olivier, Yang, Julia G., Lee, Calvin, Jacoby, Kyle, Bernstein, Irwin, Kiem, Hans-Peter, Scharenberg, Andrew, Rawlings, David J.
Publicado 2018