Canavan Disease as a Model for Gene Therapy-Mediated Myelin Repair

por Lotun, Anoushka, Gessler, Dominic J., Gao, Guangping
Publicado 2021

Editorial: Myelin Repair: At the Crossing-Lines of Myelin Biology and Gene Therapy

por Fröhlich, Dominik, Gessler, Dominic J., Klugmann, Matthias
Publicado 2022

Adeno-associated virus serotype rh.10 displays strong muscle tropism following intraperitoneal delivery

por Ai, Jianzhong, Li, Jia, Gessler, Dominic J., Su, Qin, Wei, Qiang, Li, Hong, Gao, Guangping
Publicado 2017

Transcriptome Profiling of Neovascularized Corneas Reveals miR-204 as a Multi-target Biotherapy Deliverable by rAAVs

por Lu, Yi, Tai, Phillip W.L., Ai, Jianzhong, Gessler, Dominic J., Su, Qin, Yao, Xieyi, Zheng, Qiang, Zamore, Phillip D., Xu, Xun, Gao, Guangping
Publicado 2018

A Rationally Engineered Capsid Variant of AAV9 for Systemic CNS-Directed and Peripheral Tissue-Detargeted Gene Delivery in Neonates

por Wang, Dan, Li, Shaoyong, Gessler, Dominic J., Xie, Jun, Zhong, Li, Li, Jia, Tran, Karen, Van Vliet, Kim, Ren, Lingzhi, Su, Qin, He, Ran, Goetzmann, Jason E., Flotte, Terence R., Agbandje-McKenna, Mavis, Gao, Guangping
Publicado 2018

Structural characterization of a novel human adeno-associated virus capsid with neurotropic properties

por Hsu, Hung-Lun, Brown, Alexander, Loveland, Anna B., Lotun, Anoushka, Xu, Meiyu, Luo, Li, Xu, Guangchao, Li, Jia, Ren, Lingzhi, Su, Qin, Gessler, Dominic J., Wei, Yuquan, Tai, Phillip W. L., Korostelev, Andrei A., Gao, Guangping
Publicado 2020

GammaTile® brachytherapy in the treatment of recurrent glioblastomas

por Gessler, Dominic J, Neil, Elizabeth C, Shah, Rena, Levine, Joseph, Shanks, James, Wilke, Christopher, Reynolds, Margaret, Zhang, Shunqing, Özütemiz, Can, Gencturk, Mehmet, Folkertsma, Mark, Bell, W Robert, Chen, Liam, Ferreira, Clara, Dusenbery, Kathryn, Chen, Clark C
Publicado 2021

Diseases caused by different mutations in the two alleles of a gene are treated in mice by Cas-9-induced allelic exchange.: Cas9-mediated allelic exchange repairs compound heterozy...

por Wang, Dan, Li, Jia, Song, Chun-Qing, Tran, Karen, Mou, Haiwei, Wu, Pei-Hsuan, Tai, Phillip W.L., Mendonca, Craig A., Ren, Lingzhi, Wang, Blake Y., Su, Qin, Gessler, Dominic J., Zamore, Phillip D., Xue, Wen, Gao, Guangping
Publicado 2018

Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation

por Corti, Manuela, Byrne, Barry J., Gessler, Dominic J., Thompson, Grace, Norman, Samantha, Lammers, Jenna, Coleman, Kirsten E., Liberati, Cristina, Elder, Melissa E., Escolar, Maria L., Tuna, Ibrahim S., Mesaros, Clementina, Kleiner, Gary I., Barbouth, Deborah S., Gray-Edwards, Heather L., Clement, Nathalie, Cleaver, Brian D., Gao, Guangping
Publicado 2023