Curative Cell and Gene Therapy for Osteogenesis Imperfecta

por Schindeler, Aaron, Lee, Lucinda R, O'Donohue, Alexandra K, Ginn, Samantha L, Munns, Craig F
Publicado 2022

Myoblast sensitivity and fibroblast insensitivity to osteogenic conversion by BMP-2 correlates with the expression of Bmpr-1a

por Liu, Renjing, Ginn, Samantha L, Lek, Monkol, North, Kathryn N, Alexander, Ian E, Little, David G, Schindeler, Aaron
Publicado 2009

Impact of next-generation sequencing error on analysis of barcoded plasmid libraries of known complexity and sequence

por Deakin, Claire T., Deakin, Jeffrey J., Ginn, Samantha L., Young, Paul, Humphreys, David, Suter, Catherine M., Alexander, Ian E., Hallwirth, Claus V.
Publicado 2014

Efficient in vivo editing of OTC-deficient patient-derived primary human hepatocytes

por Ginn, Samantha L., Amaya, Anais K., Liao, Sophia H.Y., Zhu, Erhua, Cunningham, Sharon C., Lee, Michael, Hallwirth, Claus V., Logan, Grant J., Tay, Szun S., Cesare, Anthony J., Pickett, Hilda A., Grompe, Markus, Dilworth, Kimberley, Lisowski, Leszek, Alexander, Ian E.
Publicado 2019

Limiting Thymic Precursor Supply Increases the Risk of Lymphoid Malignancy in Murine X-Linked Severe Combined Immunodeficiency

por Ginn, Samantha L., Hallwirth, Claus V., Liao, Sophia H.Y., Teber, Erdahl T., Arthur, Jonathan W., Wu, Jianmin, Lee, Hong Ching, Tay, Szun S., Hu, Min, Reddel, Roger R., McCormack, Matthew P., Thrasher, Adrian J., Cavazzana, Marina, Alexander, Stephen I., Alexander, Ian E.
Publicado 2017

Codon-Optimization of Wild-Type Adeno-Associated Virus Capsid Sequences Enhances DNA Family Shuffling while Conserving Functionality

por Cabanes-Creus, Marti, Ginn, Samantha L., Amaya, Anais K., Liao, Sophia H.Y., Westhaus, Adrian, Hallwirth, Claus V., Wilmott, Patrick, Ward, Jason, Dilworth, Kimberley L., Santilli, Giorgia, Rybicki, Arkadiusz, Nakai, Hiroyuki, Thrasher, Adrian J., Filip, Adrian C., Alexander, Ian E., Lisowski, Leszek
Publicado 2018

Coherence analysis discriminates between retroviral integration patterns in CD34(+) cells transduced under differing clinical trial conditions

por Hallwirth, Claus V, Garg, Gagan, Peters, Timothy J, Kramer, Belinda A, Malani, Nirav V, Hyman, Jessica, Ruan, Xiaoan, Ginn, Samantha L, Hetherington, Nicola A, Veeravalli, Lavanya, Shahab, Atif, Ranganathan, Shoba, Wei, Chia-Lin, Liddle, Christopher, Thrasher, Adrian J, Bushman, Frederic D, Buckley, Michael J, Alexander, Ian E
Publicado 2015

Development of new adeno-associated virus capsid variants for targeted gene delivery to human cardiomyocytes

por Kok, Cindy Y., Tsurusaki, Shinya, Cabanes-Creus, Marti, Igoor, Sindhu, Rao, Renuka, Skelton, Rhys, Liao, Sophia H.Y., Ginn, Samantha L., Knight, Maddison, Scott, Suzanne, Mietzsch, Mario, Fitzsimmons, Rebecca, Miller, Jessica, Mohamed, Tamer M.A., McKenna, Robert, Chong, James J.H., Hill, Adam P., Hudson, James E., Alexander, Ian E., Lisowski, Leszek, Kizana, Eddy
Publicado 2023