Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Iduronate-2-Sulfatase in Rhesus Macaques

por Hordeaux, Juliette, Hinderer, Christian, Goode, Tamara, Buza, Elizabeth L., Bell, Peter, Calcedo, Roberto, Richman, Laura K., Wilson, James M.
Publicado 2018

Translational Feasibility of Lumbar Puncture for Intrathecal AAV Administration

por Hinderer, Christian, Katz, Nathan, Dyer, Cecilia, Goode, Tamara, Johansson, Julia, Bell, Peter, Richman, Laura, Buza, Elizabeth, Wilson, James M.
Publicado 2020

Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Human Alpha-L-Iduronidase in Rhesus Macaques

por Hordeaux, Juliette, Hinderer, Christian, Goode, Tamara, Katz, Nathan, Buza, Elizabeth L., Bell, Peter, Calcedo, Roberto, Richman, Laura K., Wilson, James M.
Publicado 2018

Impact of intravenous infusion time on AAV8 vector pharmacokinetics, safety, and liver transduction in cynomolgus macaques

por Greig, Jenny A, Nordin, Jayme ML, Bote, Erin, Makaron, Leah, Garnett, Mason E, Kattenhorn, Lisa M, Bell, Peter, Goode, Tamara, Wilson, James M
Publicado 2016

Determining the Minimally Effective Dose of a Clinical Candidate Adeno-Associated Virus Vector in a Mouse Model of Hemophilia A

por Greig, Jenny A., Smith, Melanie K., Nordin, Jayme M.L., Goode, Tamara, Chroscinski, Edward A., Buza, Elizabeth L., Schmidt, Nicole, Kattenhorn, Lisa M., Wadsworth, Samuel, Wilson, James M.
Publicado 2022

Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectors

por Horiuchi, Makoto, Hinderer, Christian J., Greig, Jenny A., Dyer, Cecilia, Buza, Elizabeth L., Bell, Peter, Chichester, Jessica A., Hayashi, Peter M., Yan, Hanying, Goode, Tamara, Wilson, James M.
Publicado 2022

Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectors

por Horiuchi, Makoto, Hinderer, Christian J., Greig, Jenny A., Dyer, Cecilia, Buza, Elizabeth L., Bell, Peter, Chichester, Jessica A., Hayashi, Peter M., Yan, Hanying, Goode, Tamara, Wilson, James M.
Publicado 2022

AAV8 Gene Therapy for Crigler-Najjar Syndrome in Macaques Elicited Transgene T Cell Responses That Are Resident to the Liver

por Greig, Jenny A., Calcedo, Roberto, Kuri-Cervantes, Leticia, Nordin, Jayme M.L., Albrecht, Jessica, Bote, Erin, Goode, Tamara, Chroscinski, Edward A., Bell, Peter, Richman, Laura K., Betts, Michael R., Wilson, James M.
Publicado 2018

Adeno-associated virus-mediated expression of human butyrylcholinesterase to treat organophosphate poisoning

por Gupta, Vibhor, Cadieux, C. Linn, McMenamin, Deirdre, Medina-Jaszek, C. Angelica, Arif, Muhammad, Ahonkhai, Omua, Wielechowski, Erik, Taheri, Maryam, Che, Yan, Goode, Tamara, Limberis, Maria P., Li, Mingyao, Cerasoli, Douglas M., Tretiakova, Anna P., Wilson, James M.
Publicado 2019