Therapeutic Strategies for Dystrophin Replacement in Duchenne Muscular Dystrophy

por Happi Mbakam, Cedric, Lamothe, Gabriel, Tremblay, Jacques P.
Publicado 2022

Prime Editing Permits the Introduction of Specific Mutations in the Gene Responsible for Duchenne Muscular Dystrophy

por Happi Mbakam, Cédric, Rousseau, Joël, Tremblay, Guillaume, Yameogo, Pouiré, Tremblay, Jacques P.
Publicado 2022

Improvements of nuclease and nickase gene modification techniques for the treatment of genetic diseases

por Lu, Yaoyao, Happi Mbakam, Cedric, Song, Bo, Bendavid, Eli, Tremblay, Jacques-P.
Publicado 2022

Prime editing optimized RTT permits the correction of the c.8713C>T mutation in DMD gene

por Happi Mbakam, Cedric, Rousseau, Joel, Lu, Yaoyao, Bigot, Anne, Mamchaoui, Kamel, Mouly, Vincent, Tremblay, Jacques P.
Publicado 2022

Prime editing strategies to mediate exon skipping in DMD gene

por Happi Mbakam, Cedric, Roustant, Jeanne, Rousseau, Joel, Yameogo, Pouire, Lu, Yaoyao, Bigot, Anne, Mamchaoui, Kamel, Mouly, Vincent, Lamothe, Gabriel, Tremblay, Jacques P.
Publicado 2023