Pegvaliase dose escalation to 80 mg daily may lead to efficacy in patients who do not exhibit an optimal response at lower doses

por Vucko, Erika R., Havens, Kirsten E., Baker, Joshua J., Burton, Barbara K.
Publicado 2022

Variable disease manifestations and metabolic management within a single family affected by ornithine transcarbamylase deficiency()

por Baker, Joshua, Hitchins, Lauren, Vucko, Erika, Havens, Kirsten, Becker, Karen, Arduini, Katherine
Publicado 2022