Preclinical Profile and Characterization of the Hepatitis B Virus Core Protein Inhibitor ABI-H0731

por Huang, Qi, Cai, Dawei, Yan, Ran, Li, Lichun, Zong, Yuhua, Guo, Lida, Mercier, Alexandre, Zhou, Yi, Tang, Ariel, Henne, Kirk, Colonno, Richard
Publicado 2020

High-Throughput Liquid Chromatography–Tandem Mass Spectrometry Quantification of Glycosaminoglycans as Biomarkers of Mucopolysaccharidosis II

por Wang, Junhua, Bhalla, Akhil, Ullman, Julie C., Fang, Meng, Ravi, Ritesh, Arguello, Annie, Thomsen, Elliot, Tsogtbaatar, Buyankhishig, Guo, Jing L., Skuja, Lukas L., Dugas, Jason C., Davis, Sonnet S., Poda, Suresh B., Gunasekaran, Kannan, Costanzo, Simona, Sweeney, Zachary K., Henry, Anastasia G., Harris, Jeffrey M., Henne, Kirk R., Astarita, Giuseppe
Publicado 2020

Iduronate-2-sulfatase transport vehicle rescues behavioral and skeletal phenotypes in a mouse model of Hunter syndrome

por Arguello, Annie, Meisner, René, Thomsen, Elliot R., Nguyen, Hoang N., Ravi, Ritesh, Simms, Jeffrey, Lo, Iris, Speckart, Jessica, Holtzman, Julia, Gill, Thomas M., Chan, Darren, Cheng, Yuhsiang, Chiu, Chi-Lu, Dugas, Jason C., Fang, Meng, Lopez, Isabel A., Solanoy, Hilda, Tsogtbaatar, Buyankhishig, Zhu, Yuda, Bhalla, Akhil, Henne, Kirk R., Henry, Anastasia G., Delucchi, Anthony, Costanzo, Simona, Harris, Jeffrey M., Diaz, Dolores, Scearce-Levie, Kimberly, Sanchez, Pascal E.
Publicado 2021

Molecular architecture determines brain delivery of a transferrin receptor–targeted lysosomal enzyme

por Arguello, Annie, Mahon, Cathal S., Calvert, Meredith E.K., Chan, Darren, Dugas, Jason C., Pizzo, Michelle E., Thomsen, Elliot R., Chau, Roni, Damo, Lorna A., Duque, Joseph, Fang, Meng, Giese, Tina, Kim, Do Jin, Liang, Nicholas, Nguyen, Hoang N., Solanoy, Hilda, Tsogtbaatar, Buyankhishig, Ullman, Julie C., Wang, Junhua, Dennis, Mark S., Diaz, Dolores, Gunasekaran, Kannan, Henne, Kirk R., Lewcock, Joseph W., Sanchez, Pascal E., Troyer, Matthew D., Harris, Jeffrey M., Scearce-Levie, Kimberly, Shan, Lu, Watts, Ryan J., Thorne, Robert G., Henry, Anastasia G., Kariolis, Mihalis S.
Publicado 2022