Epistasis between Pax6(Sey) and genetic background reinforces the value of defined hybrid mouse models for therapeutic trials

por Hickmott, Jack W., Gunawardane, Uvini, Jensen, Kimberly, Korecki, Andrea J., Simpson, Elizabeth M.
Publicado 2018

Correction: Epistasis between Pax6(Sey) and genetic background reinforces the value of defined hybrid mouse models for therapeutic trials

por Hickmott, Jack W., Gunawardane, Uvini, Jensen, Kimberly, Korecki, Andrea J., Simpson, Elizabeth M.
Publicado 2019

Germline CRISPR/Cas9-Mediated Gene Editing Prevents Vision Loss in a Novel Mouse Model of Aniridia

por Mirjalili Mohanna, Seyedeh Zeinab, Hickmott, Jack W., Lam, Siu Ling, Chiu, Nina Y., Lengyell, Tess C., Tam, Beatrice M., Moritz, Orson L., Simpson, Elizabeth M.
Publicado 2020

Human MiniPromoters for ocular-rAAV expression in ON bipolar, cone, corneal, endothelial, Müller glial, and PAX6 cells

por Korecki, Andrea J., Cueva-Vargas, Jorge L., Fornes, Oriol, Agostinone, Jessica, Farkas, Rachelle A., Hickmott, Jack W., Lam, Siu Ling, Mathelier, Anthony, Zhou, Michelle, Wasserman, Wyeth W., Di Polo, Adriana, Simpson, Elizabeth M.
Publicado 2021

Progress in Respiratory Gene Therapy

por McLachlan, Gerry, Alton, Eric W.F.W., Boyd, A. Christopher, Clarke, Nora K., Davies, Jane C., Gill, Deborah R., Griesenbach, Uta, Hickmott, Jack W., Hyde, Stephen C., Miah, Kamran M., Molina, Claudia Juarez
Publicado 2022

PAX6 MiniPromoters drive restricted expression from rAAV in the adult mouse retina

por Hickmott, Jack W, Chen, Chih-yu, Arenillas, David J, Korecki, Andrea J, Lam, Siu Ling, Molday, Laurie L, Bonaguro, Russell J, Zhou, Michelle, Chou, Alice Y, Mathelier, Anthony, Boye, Sanford L, Hauswirth, William W, Molday, Robert S, Wasserman, Wyeth W, Simpson, Elizabeth M
Publicado 2016

New MiniPromoter Ple345 (NEFL) Drives Strong and Specific Expression in Retinal Ganglion Cells of Mouse and Primate Retina

por Simpson, Elizabeth M., Korecki, Andrea J., Fornes, Oriol, McGill, Trevor J., Cueva-Vargas, Jorge Luis, Agostinone, Jessica, Farkas, Rachelle A., Hickmott, Jack W., Lam, Siu Ling, Mathelier, Anthony, Renner, Lauren M., Stoddard, Jonathan, Zhou, Michelle, Di Polo, Adriana, Neuringer, Martha, Wasserman, Wyeth W.
Publicado 2019

Twenty-Seven Tamoxifen-Inducible iCre-Driver Mouse Strains for Eye and Brain, Including Seventeen Carrying a New Inducible-First Constitutive-Ready Allele

por Korecki, Andrea J., Hickmott, Jack W., Lam, Siu Ling, Dreolini, Lisa, Mathelier, Anthony, Baker, Oliver, Kuehne, Claudia, Bonaguro, Russell J., Smith, Jillian, Tan, Chin-Vern, Zhou, Michelle, Goldowitz, Daniel, Deussing, Jan M., Stewart, A. Francis, Wasserman, Wyeth W., Holt, Robert A., Simpson, Elizabeth M.
Publicado 2019

rAAV-compatible MiniPromoters for restricted expression in the brain and eye

por de Leeuw, Charles N., Korecki, Andrea J., Berry, Garrett E., Hickmott, Jack W., Lam, Siu Ling, Lengyell, Tess C., Bonaguro, Russell J., Borretta, Lisa J., Chopra, Vikramjit, Chou, Alice Y., D’Souza, Cletus A., Kaspieva, Olga, Laprise, Stéphanie, McInerny, Simone C., Portales-Casamar, Elodie, Swanson-Newman, Magdalena I., Wong, Kaelan, Yang, George S., Zhou, Michelle, Jones, Steven J. M., Holt, Robert A., Asokan, Aravind, Goldowitz, Daniel, Wasserman, Wyeth W., Simpson, Elizabeth M.
Publicado 2016