The Application of Adeno-Associated Viral Vector Gene Therapy to the Treatment of Fragile X Syndrome

por Hampson, David R., Hooper, Alexander W. M., Niibori, Yosuke
Publicado 2019

Gene therapy using an ortholog of human fragile X mental retardation protein partially rescues behavioral abnormalities and EEG activity

por Hooper, Alexander W.M., Wong, Hayes, Niibori, Yosuke, Abdoli, Rozita, Karumuthil-Melethil, Subha, Qiao, Chunping, Danos, Olivier, Bruder, Joseph T., Hampson, David R.
Publicado 2021

CNS-dominant human FMRP isoform rescues seizures, fear, and sleep abnormalities in Fmr1-KO mice

por Wong, Hayes, Hooper, Alexander W.M., Kang, Hye Ri, Lee, Shiron J., Zhao, Jiayi, Sadhu, Chanchal, Rawat, Satinder, Gray, Steven J., Hampson, David R.
Publicado 2023

Interregulation between fragile X mental retardation protein and methyl CpG binding protein 2 in the mouse posterior cerebral cortex

por Arsenault, Jason, Hooper, Alexander W M, Gholizadeh, Shervin, Kong, Tian, Pacey, Laura K, Koxhioni, Enea, Niibori, Yosuke, Eubanks, James H, Wang, Lu-Yang, Hampson, David R
Publicado 2020