CRISPR medicine for blood disorders: Progress and challenges in delivery

por Mohammadian Gol, Tahereh, Ureña-Bailén, Guillermo, Hou, Yujuan, Sinn, Ralph, Antony, Justin S., Handgretinger, Rupert, Mezger, Markus
Publicado 2023

Somatic Reversion of a Novel IL2RG Mutation Resulting in Atypical X-Linked Combined Immunodeficiency

por Hou, Yujuan, Gratz, Hans Peter, Ureña-Bailén, Guillermo, Gratz, Paul G., Schilbach-Stückle, Karin, Renno, Tina, Güngör, Derya, Mader, Daniel A., Malenke, Elke, Antony, Justin S., Handgretinger, Rupert, Mezger, Markus
Publicado 2021

Challenges in Gene Therapy for Somatic Reverted Mosaicism in X-Linked Combined Immunodeficiency by CRISPR/Cas9 and Prime Editing

por Hou, Yujuan, Ureña-Bailén, Guillermo, Mohammadian Gol, Tahereh, Gratz, Paul Gerhard, Gratz, Hans Peter, Roig-Merino, Alicia, Antony, Justin S., Lamsfus-Calle, Andrés, Daniel-Moreno, Alberto, Handgretinger, Rupert, Mezger, Markus
Publicado 2022

Preclinical Evaluation of CRISPR-Edited CAR-NK-92 Cells for Off-the-Shelf Treatment of AML and B-ALL

por Ureña-Bailén, Guillermo, Dobrowolski, Jérôme-Maurice, Hou, Yujuan, Dirlam, Alicia, Roig-Merino, Alicia, Schleicher, Sabine, Atar, Daniel, Seitz, Christian, Feucht, Judith, Antony, Justin S., Mohammadian Gol, Tahereh, Handgretinger, Rupert, Mezger, Markus
Publicado 2022