Gene Therapy for Primary Immunodeficiency

por Houghton, Benjamin C., Booth, Claire
Publicado 2020

Lentiviral Gene Transfer Corrects Immune Abnormalities in XIAP Deficiency

por Topal, Joseph, Panchal, Neelam, Barroeta, Amairelys, Roppelt, Anna, Mudde, Annelotte, Gaspar, H. Bobby, Thrasher, Adrian J., Houghton, Benjamin C., Booth, Claire
Publicado 2022

Genome Editing With TALEN, CRISPR-Cas9 and CRISPR-Cas12a in Combination With AAV6 Homology Donor Restores T Cell Function for XLP

por Houghton, Benjamin C., Panchal, Neelam, Haas, Simone A., Chmielewski, Kay O., Hildenbeutel, Markus, Whittaker, Thomas, Mussolino, Claudio, Cathomen, Toni, Thrasher, Adrian J, Booth, Claire
Publicado 2022

Lentiviral Mediated ADA2 Gene Transfer Corrects the Defects Associated With Deficiency of Adenosine Deaminase Type 2

por Hong, Ying, Casimir, Marina, Houghton, Benjamin C., Zhang, Fang, Jensen, Barbara, Omoyinmi, Ebun, Torrance, Robert, Papadopoulou, Charalampia, Cummins, Michelle, Roderick, Marion, Thrasher, Adrian J., Brogan, Paul A., Eleftheriou, Despina
Publicado 2022