Directed differentiation of human pluripotent stem cells into mature airway epithelia expressing functional CFTR protein

por Wong, Amy P., Bear, Christine E., Chin, Stephanie, Pasceri, Peter, Thompson, Tadeo O., Huan, Ling-Jun, Ratjen, Felix, Ellis, James, Rossant, Janet
Publicado 2012

Identification of binding sites for ivacaftor on the cystic fibrosis transmembrane conductance regulator

por Laselva, Onofrio, Qureshi, Zafar, Zeng, Zhi-Wei, Petrotchenko, Evgeniy V., Ramjeesingh, Mohabir, Hamilton, C. Michael, Huan, Ling-Jun, Borchers, Christoph H., Pomès, Régis, Young, Robert, Bear, Christine E.
Publicado 2021

Orkambi® and amplifier co‐therapy improves function from a rare CFTR mutation in gene‐edited cells and patient tissue

por Molinski, Steven V, Ahmadi, Saumel, Ip, Wan, Ouyang, Hong, Villella, Adriana, Miller, John P, Lee, Po‐Shun, Kulleperuma, Kethika, Du, Kai, Di Paola, Michelle, Eckford, Paul DW, Laselva, Onofrio, Huan, Ling Jun, Wellhauser, Leigh, Li, Ellen, Ray, Peter N, Pomès, Régis, Moraes, Theo J, Gonska, Tanja, Ratjen, Felix, Bear, Christine E
Publicado 2017