Long-term administration of intravenous Trappsol® Cyclo™ (HP-β-CD) results in clinical benefits and stabilization or slowing of disease progression in patients with Niemann-Pick di...

por Sharma, Reena, Hastings, Caroline, Staretz-Chacham, Orna, Raiman, Julian, Paucar, Martin, Spiegel, Ronen, Murray, Bryan, Hurst, Bryan, Liu, Benny, Kjems, Lise, Hrynkow, Sharon
Publicado 2023