Real-World Data on Access to Standards of Care for People With Spinal Muscular Atrophy in the UK

por Muni-Lofra, Robert, Murphy, Lindsay B., Adcock, Kate, Farrugia, Maria E., Irwin, Joseph, Lilleker, James B., McConville, John, Merrison, Andria, Parton, Matt, Ryburn, Liz, Scoto, Mariacristina, Marini-Bettolo, Chiara, Mayhew, Anna
Publicado 2022

Guidance in Social and Ethical Issues Related to Clinical, Diagnostic Care and Novel Therapies for Hereditary Neuromuscular Rare Diseases: “Translating“ the Translational

por McCormack, Pauline, Woods, Simon, Aartsma-Rus, Annemieke, Hagger, Lynn, Herczegfalvi, Agnes, Heslop, Emma, Irwin, Joseph, Kirschner, Janbernd, Moeschen, Patrick, Muntoni, Francesco, Ouillade, Marie-Christine, Rahbek, Jes, Rehmann-Sutter, Christoph, Rouault, Francoise, Sejersen, Thomas, Vroom, Elizabeth, Straub, Volker, Bushby, Kate, Ferlini, Alessandra
Publicado 2013