SERPINA1 mRNA as a Treatment for Alpha-1 Antitrypsin Deficiency

por Connolly, Brendan, Isaacs, Cleo, Cheng, Lei, Asrani, Kirtika H., Subramanian, Romesh R.
Publicado 2018

G6PC mRNA Therapy Positively Regulates Fasting Blood Glucose and Decreases Liver Abnormalities in a Mouse Model of Glycogen Storage Disease 1a

por Roseman, Daniel S., Khan, Tayeba, Rajas, Fabienne, Jun, Lucy S., Asrani, Kirtika H., Isaacs, Cleo, Farelli, Jeremiah D., Subramanian, Romesh R.
Publicado 2018