Myostatin inhibition in combination with antisense oligonucleotide therapy improves outcomes in spinal muscular atrophy

por Zhou, Haiyan, Meng, Jinhong, Malerba, Alberto, Catapano, Francesco, Sintusek, Palittiya, Jarmin, Susan, Feng, Lucy, Lu‐Nguyen, Ngoc, Sun, Lianwen, Mariot, Virginie, Dumonceaux, Julie, Morgan, Jennifer E., Gissen, Paul, Dickson, George, Muntoni, Francesco
Publicado 2020

piggyBac transposons expressing full-length human dystrophin enable genetic correction of dystrophic mesoangioblasts

por Loperfido, Mariana, Jarmin, Susan, Dastidar, Sumitava, Di Matteo, Mario, Perini, Ilaria, Moore, Marc, Nair, Nisha, Samara-Kuko, Ermira, Athanasopoulos, Takis, Tedesco, Francesco Saverio, Dickson, George, Sampaolesi, Maurilio, VandenDriessche, Thierry, Chuah, Marinee K.
Publicado 2016

Nuclear poly(A)-binding protein aggregates misplace a pre-mRNA outside of SC35 speckle causing its abnormal splicing

por Klein, Pierre, Oloko, Martine, Roth, Fanny, Montel, Valérie, Malerba, Alberto, Jarmin, Susan, Gidaro, Teresa, Popplewell, Linda, Perie, Sophie, Lacau St Guily, Jean, de la Grange, Pierre, Antoniou, Michael N., Dickson, George, Butler-Browne, Gillian, Bastide, Bruno, Mouly, Vincent, Trollet, Capucine
Publicado 2016