The HIV-1 Rev/RRE system is required for HIV-1 5' UTR cis elements to augment encapsidation of heterologous RNA into HIV-1 viral particles

por Cockrell, Adam S, van Praag, Henriette, Santistevan, Nicholas, Ma, Hong, Kafri, Tal
Publicado 2011

Generation of a stable packaging cell line producing high-titer PPT-deleted integration-deficient lentiviral vectors

por Hu, Peirong, Li, Yedda, Sands, Mark S, McCown, Thomas, Kafri, Tal
Publicado 2015

Inadvertent Transfer of Murine VL30 Retrotransposons to CAR-T Cells

por Lee, Sung Hyun, Hao, Yajing, Gui, Tong, Dotti, Gianpietro, Savoldo, Barbara, Zou, Fei, Kafri, Tal
Publicado 2022

Harnessing the Anti-Tumor Mediators in Mast Cells as a New Strategy for Adoptive Cell Transfer for Cancer

por Fereydouni, Mohammad, Motaghed, Mona, Ahani, Elnaz, Kafri, Tal, Dellinger, Kristen, Metcalfe, Dean D., Kepley, Christopher L.
Publicado 2022

Targeted Knockdown of Overexpressed VEGFA or VEGF164 in Müller cells maintains retinal function by triggering different signaling mechanisms

por Becker, Silke, Wang, Haibo, Simmons, Aaron B., Suwanmanee, Thipparat, Stoddard, Gregory J., Kafri, Tal, Hartnett, M. Elizabeth
Publicado 2018

Toward Personalized Gene Therapy: Characterizing the Host Genetic Control of Lentiviral-Vector-Mediated Hepatic Gene Delivery

por Suwanmanee, Thipparat, Ferris, Martin T., Hu, Peirong, Gui, Tong, Montgomery, Stephanie A., Pardo-Manuel de Villena, Fernando, Kafri, Tal
Publicado 2017

Superior lentiviral vectors designed for BSL-0 environment abolish vector mobilization.

por Hu, Peirong, Bi, Yanmin, Ma, Hong, Suwanmanee, Thipparat, Zeithaml, Brian, Fry, Nate J., Kohn, Donald B., Kafri, Tal
Publicado 2018

AAV Exploits Subcellular Stress Associated with Inflammation, Endoplasmic Reticulum Expansion, and Misfolded Proteins in Models of Cystic Fibrosis

por Johnson, Jarrod S., Gentzsch, Martina, Zhang, Liqun, Ribeiro, Carla M. P., Kantor, Boris, Kafri, Tal, Pickles, Raymond J., Samulski, R. Jude
Publicado 2011

CCR5 Gene Editing of Resting CD4(+) T Cells by Transient ZFN Expression From HIV Envelope Pseudotyped Nonintegrating Lentivirus Confers HIV-1 Resistance in Humanized Mice

por Yi, Guohua, Choi, Jang Gi, Bharaj, Preeti, Abraham, Sojan, Dang, Ying, Kafri, Tal, Alozie, Ogechika, Manjunath, Manjunath N, Shankar, Premlata
Publicado 2014

Dominant-Negative Androgen Receptor Inhibition of Intracrine Androgen-Dependent Growth of Castration-Recurrent Prostate Cancer

por Titus, Mark A., Zeithaml, Brian, Kantor, Boris, Li, Xiangping, Haack, Karin, Moore, Dominic T., Wilson, Elizabeth M., Mohler, James L., Kafri, Tal
Publicado 2012

Gene therapy knockdown of VEGFR2 in retinal endothelial cells to treat retinopathy

por Simmons, Aaron B., Bretz, Colin A., Wang, Haibo, Kunz, Eric, Hajj, Kassem, Kennedy, Carson, Yang, Zhihong, Suwanmanee, Thipparat, Kafri, Tal, Hartnett, M. Elizabeth
Publicado 2018

Correction to: Gene therapy knockdown of VEGFR2 in retinal endothelial cells to treat retinopathy

por Simmons, Aaron B., Bretz, Colin A., Wang, Haibo, Kunz, Eric, Hajj, Kassem, Kennedy, Carson, Yang, Zhihong, Suwanmanee, Thipparat, Kafri, Tal, Hartnett, M. Elizabeth
Publicado 2018

Hematopoietic Stem cell transplantation and lentiviral vector‐based gene therapy for Krabbe's disease: Present convictions and future prospects

por Hu, Peirong, Li, Yedda, Nikolaishvili‐Feinberg, Nana, Scesa, Giuseppe, Bi, Yanmin, Pan, Dao, Moore, Dominic, Bongarzone, Ernesto R., Sands, Mark S., Miller, Ryan, Kafri, Tal
Publicado 2016

Human Tumor Targeted Cytotoxic Mast Cells for Cancer Immunotherapy

por Fereydouni, Mohammad, Ahani, Elnaz, Desai, Parth, Motaghed, Mona, Dellinger, Anthony, Metcalfe, Dean D., Yin, Yuzhi, Lee, Sung Hyun, Kafri, Tal, Bhatt, Aadra P., Dellinger, Kristen, Kepley, Christopher L.
Publicado 2022

Pharmacokinetics and Efficacy of PEGylated Liposomal Doxorubicin in an Intracranial Model of Breast Cancer

por Anders, Carey K., Adamo, Barbara, Karginova, Olga, Deal, Allison M., Rawal, Sumit, Darr, David, Schorzman, Allison, Santos, Charlene, Bash, Ryan, Kafri, Tal, Carey, Lisa, Miller, C. Ryan, Perou, Charles M., Sharpless, Norman, Zamboni, William C.
Publicado 2013

Employing a Gain-of-Function Factor IX Variant R338L to Advance the Efficacy and Safety of Hemophilia B Human Gene Therapy: Preclinical Evaluation Supporting an Ongoing Adeno-Assoc...

por Monahan, Paul E., Sun, Junjiang, Gui, Tong, Hu, Genlin, Hannah, William B., Wichlan, David G., Wu, Zhijian, Grieger, Joshua C., Li, Chengwen, Suwanmanee, Thipparat, Stafford, Darrel W., Booth, Carmen J., Samulski, Jade J., Kafri, Tal, McPhee, Scott W.J., Samulski, R. Jude
Publicado 2015

A Single Synonymous Variant (c.354G>A [p.P118P]) in ADAMTS13 Confers Enhanced Specific Activity

por Hunt, Ryan, Hettiarachchi, Gaya, Katneni, Upendra, Hernandez, Nancy, Holcomb, David, Kames, Jacob, Alnifaidy, Redab, Lin, Brian, Hamasaki-Katagiri, Nobuko, Wesley, Aaron, Kafri, Tal, Morris, Christina, Bouché, Laura, Panico, Maria, Schiller, Tal, Ibla, Juan, Bar, Haim, Ismail, Amra, Morris, Howard, Komar, Anton, Kimchi-Sarfaty, Chava
Publicado 2019

Structural, functional, and immunogenicity implications of F9 gene recoding

por Katneni, Upendra K., Alexaki, Aikaterini, Hunt, Ryan C., Hamasaki-Katagiri, Nobuko, Hettiarachchi, Gaya K., Kames, Jacob M., McGill, Joseph R., Holcomb, David D., Athey, John C., Lin, Brian, Parunov, Leonid A., Kafri, Tal, Lu, Qi, Peters, Robert, Ovanesov, Mikhail V., Freedberg, Darón I., Bar, Haim, Komar, Anton A., Sauna, Zuben E., Kimchi-Sarfaty, Chava
Publicado 2022

Content and Performance of the MiniMUGA Genotyping Array: A New Tool To Improve Rigor and Reproducibility in Mouse Research

por Sigmon, John Sebastian, Blanchard, Matthew W., Baric, Ralph S., Bell, Timothy A., Brennan, Jennifer, Brockmann, Gudrun A., Burks, A. Wesley, Calabrese, J. Mauro, Caron, Kathleen M., Cheney, Richard E., Ciavatta, Dominic, Conlon, Frank, Darr, David B., Faber, James, Franklin, Craig, Gershon, Timothy R., Gralinski, Lisa, Gu, Bin, Gaines, Christiann H., Hagan, Robert S., Heimsath, Ernest G., Heise, Mark T., Hock, Pablo, Ideraabdullah, Folami, Jennette, J. Charles, Kafri, Tal, Kashfeen, Anwica, Kulis, Mike, Kumar, Vivek, Linnertz, Colton, Livraghi-Butrico, Alessandra, Lloyd, K. C. Kent, Lutz, Cathleen, Lynch, Rachel M., Magnuson, Terry, Matsushima, Glenn K., McMullan, Rachel, Miller, Darla R., Mohlke, Karen L., Moy, Sheryl S., Murphy, Caroline E. Y., Najarian, Maya, O’Brien, Lori, Palmer, Abraham A., Philpot, Benjamin D., Randell, Scott H., Reinholdt, Laura, Ren, Yuyu, Rockwood, Steve, Rogala, Allison R., Saraswatula, Avani, Sassetti, Christopher M., Schisler, Jonathan C., Schoenrock, Sarah A., Shaw, Ginger D., Shorter, John R., Smith, Clare M., St. Pierre, Celine L., Tarantino, Lisa M., Threadgill, David W., Valdar, William, Vilen, Barbara J., Wardwell, Keegan, Whitmire, Jason K., Williams, Lucy, Zylka, Mark J., Ferris, Martin T., McMillan, Leonard, Manuel de Villena, Fernando Pardo
Publicado 2020