A pathogenic proteolysis–resistant huntingtin isoform induced by an antisense oligonucleotide maintains huntingtin function

por Kim, Hyeongju, Lenoir, Sophie, Helfricht, Angela, Jung, Taeyang, Karneva, Zhana K., Lee, Yejin, Beumer, Wouter, van der Horst, Geert B., Anthonijsz, Herma, Buil, Levi C.M., van der Ham, Frits, Platenburg, Gerard J., Purhonen, Pasi, Hebert, Hans, Humbert, Sandrine, Saudou, Frédéric, Klein, Pontus, Song, Ji-Joon
Publicado 2022