Cas9-induced single cut enables highly efficient and template-free repair of a muscular dystrophy causing founder mutation

por Müthel, Stefanie, Marg, Andreas, Ignak, Busem, Kieshauer, Janine, Escobar, Helena, Stadelmann, Christian, Spuler, Simone
Publicado 2023

Human primary muscle stem cells regenerate injured urethral sphincter in athymic rats

por Bekele, Biniam M., Schöwel‐Wolf, Verena, Kieshauer, Janine, Marg, Andreas, Busjahn, Andreas, Davis, Sarah, Nugent, Gayle, Ebert, Anne‐Karoline, Spuler, Simone
Publicado 2022

Base editing repairs an SGCA mutation in human primary muscle stem cells

por Escobar, Helena, Krause, Anne, Keiper, Sandra, Kieshauer, Janine, Müthel, Stefanie, de Paredes, Manuel García, Metzler, Eric, Kühn, Ralf, Heyd, Florian, Spuler, Simone
Publicado 2021

Human muscle-derived CLEC14A-positive cells regenerate muscle independent of PAX7

por Marg, Andreas, Escobar, Helena, Karaiskos, Nikos, Grunwald, Stefanie A., Metzler, Eric, Kieshauer, Janine, Sauer, Sascha, Pasemann, Diana, Malfatti, Edoardo, Mompoint, Dominique, Quijano-Roy, Susanna, Boltengagen, Anastasiya, Schneider, Joanna, Schülke, Markus, Kunz, Séverine, Carlier, Robert, Birchmeier, Carmen, Amthor, Helge, Spuler, Andreas, Kocks, Christine, Rajewsky, Nikolaus, Spuler, Simone
Publicado 2019