BB-301: a silence and replace AAV-based vector for the treatment of oculopharyngeal muscular dystrophy

por Strings-Ufombah, Vanessa, Malerba, Alberto, Kao, Shih-Chu, Harbaran, Sonal, Roth, Fanny, Cappellari, Ornella, Lu-Nguyen, Ngoc, Takahashi, Keiko, Mukadam, Sophie, Kilfoil, Georgina, Kloth, Claudia, Roelvink, Petrus, Dickson, George, Trollet, Capucine, Suhy, David
Publicado 2021

P1167: TREATMENT OF RELAPSED/REFRACTORY HGBCL WITH MYC REARRANGEMENT: A MULTICENTER, OPEN-LABEL, PHASE 2 STUDY OF PC-002(SEPB)，A FIRST-IN-CLASS INHIBITOR OF DEUBIQUITINASES TARGETI...

por Yoon, Sung-Soo, LI, Zhiming, Zhou, Keshu, Zhou, Xiaoxi, Guo, Ye, Zhang, Huilai, Eom, Ki-Seong, Jin Kim, Seok, Yong Oh, Sung, Lim, Sungnam, Youssoufian, Hagop, Jiang, Vernon C, Huang, Zanchun, Kilfoil, Georgina, Wang, Xin, Cao, Zhixiang, LI, Xiang, Wu, Alexander, Chen, Yiyou, Song, Yuqin
Publicado 2023