Lack of germline transmission in male mice following a single intravenous administration of AAV5-hFVIII-SQ gene therapy

por Fonck, Carlos, Su, Cheng, Arens, Jeremy, Koziol, Elli, Srimani, Jaydeep, Henshaw, Joshua, Van Tuyl, Andrea, Chandra, Sundeep, Vettermann, Christian, O’Neill, Charles A.
Publicado 2022

Ultra-sensitive AAV capsid detection by immunocapture-based qPCR following factor VIII gene transfer

por Sandza, Krystal, Clark, Annie, Koziol, Elli, Akeefe, Hassibullah, Yang, Fan, Holcomb, Jennifer, Patton, Kathryn, Hammon, Kevin, Mitchell, Nina, Wong, Wing Y., Zoog, Stephen J., Kim, Benjamin, Henshaw, Joshua, Vettermann, Christian
Publicado 2021