The Case for the Use of Patient and Caregiver Perception of Change Assessments in Rare Disease Clinical Trials: A Methodologic Overview

por Contesse, Marielle G., Valentine, James E., Wall, Tracy E., Leffler, Mindy G.
Publicado 2019

Adapting traditional content validation methods to fit purpose: an example with a novel video assessment and training materials in Duchenne muscular dystrophy (DMD)

por White, Michelle K., Leffler, Mindy, Rychlec, Kaitlin, Jones, Chris, McSherry, Christine, Walker, Linsey, Kosinski, Mark
Publicado 2019

Reliability and construct validity of the Duchenne Video Assessment

por Contesse, Marielle G., Sapp, Amber T. L., Apkon, Susan D., Lowes, Linda P., Dalle Pazze, Laura, Leffler, Mindy G.
Publicado 2021

Development of Duchenne Video Assessment scorecards to evaluate ease of movement among those with Duchenne muscular dystrophy

por Contesse, Marielle G., Lowes, Linda P., White, Michelle K., Dalle Pazze, Laura, McSherry, Christine, Alfano, Lindsay N., Iammarino, Megan, Reash, Natalie, Bonarrigo, Kelly, Kiefer, Michael, Laubscher, Katie, McIntyre, Melissa, Mockler, Shelley, Nelson, Leslie, Vogel, Leslie, Leffler, Mindy G.
Publicado 2022