Isogenic GAA-KO Murine Muscle Cell Lines Mimicking Severe Pompe Mutations as Preclinical Models for the Screening of Potential Gene Therapy Strategies

por Aguilar-González, Araceli, González-Correa, Juan Elías, Barriocanal-Casado, Eliana, Ramos-Hernández, Iris, Lerma-Juárez, Miguel A., Greco, Sara, Rodríguez-Sevilla, Juan José, Molina-Estévez, Francisco Javier, Montalvo-Romeral, Valle, Ronzitti, Giuseppe, Sánchez-Martín, Rosario María, Martín, Francisco, Muñoz, Pilar
Publicado 2022