Rescue of splicing-mediated intron loss maximizes expression in lentiviral vectors containing the human ubiquitin C promoter

por Cooper, Aaron R., Lill, Georgia R., Gschweng, Eric H., Kohn, Donald B.
Publicado 2015

Reactivating Fetal Hemoglobin Expression in Human Adult Erythroblasts Through BCL11A Knockdown Using Targeted Endonucleases

por Bjurström, Carmen F, Mojadidi, Michelle, Phillips, John, Kuo, Caroline, Lai, Stephen, Lill, Georgia R, Cooper, Aaron, Kaufman, Michael, Urbinati, Fabrizia, Wang, Xiaoyan, Hollis, Roger P, Kohn, Donald B
Publicado 2016